78 results on '"Barohn, Richard"'
Search Results
2. Safety and efficacy of arimoclomol for inclusion body myositis: a multicentre, randomised, double-blind, placebo-controlled trial
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Machado, Pedro M, primary, McDermott, Michael P, additional, Blaettler, Thomas, additional, Sundgreen, Claus, additional, Amato, Anthony A, additional, Ciafaloni, Emma, additional, Freimer, Miriam, additional, Gibson, Summer B, additional, Jones, Sarah M, additional, Levine, Todd D, additional, Lloyd, Thomas E, additional, Mozaffar, Tahseen, additional, Shaibani, Aziz I, additional, Wicklund, Matthew, additional, Rosholm, Anders, additional, Carstensen, Tim Dehli, additional, Bonefeld, Karen, additional, Jørgensen, Anders Nørkær, additional, Phonekeo, Karina, additional, Heim, Andrew J, additional, Herbelin, Laura, additional, Barohn, Richard J, additional, Hanna, Michael G, additional, Dimachkie, Mazen M, additional, Dimachkie, Mazen, additional, Statland, Jeffrey, additional, Pasnoor, Mamatha, additional, Jawdat, Omar, additional, Heim, Andrew, additional, Ciersdorff, Ali, additional, Sasidharan, Sandhya, additional, Currence, Melissa, additional, Levine, Todd, additional, Otutoa, Rebecca, additional, Cooper, Angelina, additional, Habib, Ali, additional, Cauchi, Jonathan, additional, Ung, Shannon, additional, Mathew, Veena, additional, Hernandez, Isela, additional, Gibson, Summer, additional, Bromberg, Mark, additional, Mahoney, Kyle, additional, Neate, Crystal, additional, Janecki, Teresa, additional, Papadakis, Mike, additional, Kaschalk, MacKenzie, additional, Heintzman, Sarah, additional, Baines, Brenna, additional, Vareldzis, Alexa, additional, Hyslop, Emily, additional, Blume, Brianna, additional, Luebbe, Elizabeth, additional, Eichinger, Katy, additional, Martens, William, additional, Gregory, Stephanie, additional, Janciuras, Joanne, additional, Amato, Anthony, additional, Doughty, Christopher, additional, Roe, Kristen, additional, Flynn, Patricia, additional, Russo, Emily, additional, Lloyd, Thomas, additional, Albayda, Jemima, additional, Tiniakou, Eleni, additional, Thomas, Simone, additional, Jones, Sarah, additional, Solorzano, Guillermo, additional, Elliott, Matthew, additional, Burns, Ted, additional, Crowell, Allison, additional, Eggleston, Deborah, additional, Wagoner, Mary, additional, Shaibani, Aziz, additional, Oates, Chantae, additional, Machado, Pedro, additional, Hanna, Michael, additional, Greensmith, Linda, additional, Ahmed, Mhoriam, additional, Vivekanandam, Vinojini, additional, Appleby, Matthew, additional, Ransley, George, additional, Eshun, Edwin Eshun, additional, Skorupinska, Iwona, additional, Germain, Louise, additional, Laxa, Ana Marie, additional, Pontes, Joana Roca, additional, Bellin, Anna, additional, and Anifowoshe, Dolapo, additional
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- 2023
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3. Conducting a bayesian multi-armed trial with response adaptive randomization for comparative effectiveness of medications for CSPN
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Brown, Alexandra R., primary, Gajewski, Byron J., additional, Mudaranthakam, Dinesh Pal, additional, Pasnoor, Mamatha, additional, Dimachkie, Mazen M., additional, Jawdat, Omar, additional, Herbelin, Laura, additional, Mayo, Matthew S., additional, and Barohn, Richard J., additional
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- 2023
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4. Zilucoplan in immune-mediated necrotising myopathy: a phase 2, randomised, double-blind, placebo-controlled, multicentre trial
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Mammen, Andrew L, primary, Amato, Anthony A, additional, Dimachkie, Mazen M, additional, Chinoy, Hector, additional, Hussain, Yessar, additional, Lilleker, James B, additional, Pinal-Fernandez, Iago, additional, Allenbach, Yves, additional, Boroojerdi, Babak, additional, Vanderkelen, Mark, additional, Delicha, Eumorphia Maria, additional, Koendgen, Harold, additional, Farzaneh-Far, Ramin, additional, Duda, Petra W, additional, Sayegh, Camil, additional, Benveniste, Olivier, additional, Amato, Anthony A., additional, Biliciler, Suur, additional, Dimachkie, Mazen M., additional, Edmundson, Christyn, additional, Freimer, Miriam, additional, Geraci, Anthony, additional, Machado, Pedro, additional, Mammen, Andrew L., additional, Mozaffar, Tahseen, additional, Soltanzadeh, Payam, additional, Suresh, Niraja, additional, van der Kooi, Anneke, additional, Appleby, Matthew, additional, Barohn, Richard J, additional, Champtiaux, Nicolas, additional, Doughty, Christopher, additional, Farias, Jerrica, additional, Farmakidis, Constantine, additional, Habib, Ali A., additional, Karam, Chafic, additional, Lilleker, James, additional, Lorusso, Samantha, additional, Pasnoor, Mamatha, additional, Querin, Giorgia, additional, Raaphorst, Joost, additional, Ransley, George, additional, Saba, Sami, additional, Sheikh, Kazim, additional, Snedden, Andrew, additional, Statland, Jeffrey, additional, and Vu, Tuan, additional
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- 2023
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5. LRP4 antibody testing in myasthenia gravis
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Racke, Michael K., primary, Batish, Sat Dev, additional, Lisak, Robert P., additional, and Barohn, Richard J., additional
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- 2022
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6. Health related quality of life in young, steroid-naïve boys with Duchenne muscular dystrophy
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Campbell, Craig, primary, McColl, Elaine, additional, McDermott, Michael P., additional, Martens, William B., additional, Guglieri, Michela, additional, Griggs, Robert C., additional, Straub, Volker, additional, Childs, Anne-Marie, additional, Ciafaloni, Emma, additional, Shieh, Perry B., additional, Spinty, Stefan, additional, Butterfield, Russell J., additional, Horrocks, Iain, additional, Roper, Helen, additional, Maggi, Lorenzo, additional, Baranello, Giovanni, additional, Flanigan, Kevin M., additional, Kuntz, Nancy L., additional, Manzur, Adnan Y., additional, Darras, Basil T., additional, Kang, Peter, additional, Mah, Jean K., additional, Mongini, Tiziana, additional, Ricci, Federica, additional, Morrison, Leslie, additional, Krzesniak-Swinarska, Monika, additional, von der Hagen, Maja, additional, Finkel, Richard S., additional, Kumar, Ashutosh, additional, Wicklund, Matthew, additional, McDonald, Craig M., additional, Henricson, Erik K., additional, Schara-Schmidt, Ulrike, additional, Wilichowski, Ekkehard, additional, Barohn, Richard J., additional, Statland, Jeffrey, additional, Kirschner, Janbernd, additional, Vita, Giuseppe, additional, Vita, Gian Luca, additional, Howard, James F., additional, Hughes, Imelda, additional, McMillan, Hugh J., additional, Pegoraro, Elena, additional, Bello, Luca, additional, Burnette, W. Bryan, additional, Thangarajh, Mathula, additional, and Chang, Taeun, additional
- Published
- 2021
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7. Safety, efficacy, and tolerability of efgartigimod in patients with generalised myasthenia gravis (ADAPT): a multicentre, randomised, placebo-controlled, phase 3 trial
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Howard, James F, primary, Bril, Vera, additional, Vu, Tuan, additional, Karam, Chafic, additional, Peric, Stojan, additional, Margania, Temur, additional, Murai, Hiroyuki, additional, Bilinska, Malgorzata, additional, Shakarishvili, Roman, additional, Smilowski, Marek, additional, Guglietta, Antonio, additional, Ulrichts, Peter, additional, Vangeneugden, Tony, additional, Utsugisawa, Kimiaki, additional, Verschuuren, Jan, additional, Mantegazza, Renato, additional, De Bleecker, Jan L., additional, De Koning, Kathy, additional, De Mey, Katrien, additional, De Pue, Annelien, additional, Mercelis, Rudolf, additional, Wyckmans, Maren, additional, Vinck, Caroline, additional, Wagemaekers, Linda, additional, Baets, Jonathan, additional, Ng, Eduardo, additional, Shabanpour, Jafar, additional, Daniyal, Lubna, additional, Mannan, Shabber, additional, Katzberg, Hans D., additional, Genge, Angela, additional, Siddiqi, Zaeem, additional, Junkerová, Jana, additional, Horakova, Jana, additional, Reguliova, Katerina, additional, Tyblova, Michaela, additional, Jurajdova, Ivana, additional, Novakova, Iveta, additional, Jakubikova, Michala, additional, Pitha, Jiri, additional, Vohanka, Stanislav, additional, Havelkova, Katerina, additional, Horak, Tomas, additional, Bednarik, Josef, additional, Horakova, Mageda, additional, Meisel, Andreas, additional, Remstedt, Dike, additional, Heibutzki, Claudia, additional, Kohler, Siegfried, additional, Gerischer, Lea, additional, Hoffman, Sarah, additional, Stascheit, Frauke, additional, Vissing, John, additional, Zafirakos, Lizzie, additional, Khatri, Kuldeep Kumar, additional, Autzen, Anne, additional, Godtfeldt Stemmerik, Mads Peter, additional, Andersen, Henning, additional, Attarian, Shahram, additional, Salort-Campana, Emmanuelle, additional, Delmont, Emilien, additional, Grapperon, Aude-Marie, additional, Kouton, Ludivine, additional, Tsiskaridze, Alexander, additional, Rózsa, Csilla, additional, Jakab, Gedeonne Margo, additional, Toth, Szilvia, additional, Szabo, Gyorgyi, additional, Bors, David, additional, Szabo, Eniko, additional, Campanella, Angela, additional, Vanoli, Fiammetta, additional, Frangiamore, Rita, additional, Antozzi, Carlo, additional, Bonanno, Silvia, additional, Maggi, Lorenzo, additional, Giossi, Riccardo, additional, Saccà, Francesco, additional, Marsili, Angela, additional, Pane, Chiara, additional, Puorro, Giorgia, additional, Reia, Antonio, additional, Antonini, Giovanni, additional, Alfieri, Girolamo, additional, Morino, Stefania, additional, Garibaldi, Matteo, additional, Fionda, Laura, additional, Leonardi, Luca, additional, Konno, Shingo, additional, Uzawa, Akiyuki, additional, Sakuma, Kaoru, additional, Watanabe, Chiho, additional, Ozawa, Yukiko, additional, Yasuda, Manato, additional, Onishi, Yosuke, additional, Samukawa, Makoto, additional, Tsuda, Tomoko, additional, Suzuki, Yasushi, additional, Ishida, Sayaka, additional, Watanabe, Genya, additional, Takahashi, Masanori, additional, Nakamura, Hiroko, additional, Sugano, Erina, additional, Kubota, Tomoya, additional, Imai, Tomihiro, additional, Suzuki., Mari, additional, Mori, Ayako, additional, Yamamoto, Daisuke, additional, Ikeda, Kazuna, additional, Hisahara, Shin, additional, Masuda, Masayuki, additional, Takaki, Miki, additional, Minemoto, Kanako, additional, Ido, Nobuhiro, additional, Naito, Makiko, additional, Okubo, Yoshihiko, additional, Sugimoto, Takamichi, additional, Takematsu, Yuka, additional, Kamei, Ayumi, additional, Shimizu, Mihiro, additional, Naito, Hiroyuki, additional, Nomura, Eiichi, additional, Van Heur, Marjolein, additional, Peters, Anne-Marie, additional, Tannemaat, Martijn, additional, Ruiter, Annabel, additional, Keene, Kevin, additional, Halas, Marek, additional, Szczudlik, Andrzej, additional, Pinkosz, Marta, additional, Frasinska, Monika, additional, Zwolinska, Grazyna, additional, Kostera-Pruszczyk, Anna, additional, Golenia, Aleksandra, additional, Szczudlik, Piotr, additional, Szczechowski, Lech, additional, Pasko, Aneta, additional, Poverennova, Irina, additional, Urtaeva, Lubov, additional, Kuznetsova, Nadezhda, additional, Romanova, Tatiana, additional, Nadezhda, Malkova, additional, Lapochka, Elena, additional, Korobko, Denis, additional, Vergunova, Ilona, additional, Melnikova, Anna, additional, Bulatova, Ekaterina, additional, Antipenko, Elena, additional, Basta, Ivana, additional, Bozovic, Ivo, additional, Lavrnic, Dragana, additional, Stojanovic, Vidosava Rakocevic, additional, Beydoun, Said, additional, Akhter, Salma, additional, Malekniazi, Ali, additional, Darki, Leila, additional, Pimentel, Norianne, additional, Cannon, Victoria, additional, Chopra, Manisha, additional, Traub, Rebecca, additional, Mozaffar, Tahseen, additional, Hernandez, Isela, additional, Turner, Ivonne, additional, Habib, Ali, additional, Goyal, Namita, additional, Kak, Manisha, additional, Velasquez, Erik, additional, Lam, Lucy, additional, Suresh, Niraja, additional, Farias, Jerrica, additional, Jones, Sarah, additional, Wagoner, Mary, additional, Eggleston, Debbie, additional, Bertorini, Tulio, additional, Benzel, Cindy, additional, Henegar, Robert, additional, Pillai, Rekha, additional, Bharavaju-Sanka, Ratna, additional, Paiz, Carolyn, additional, Jackson, Carlayne, additional, Ruzhansky, Katherine, additional, Dimitrova, Diana, additional, Visser, Amy, additional, Chahin, Nizar, additional, Levine, Todd, additional, Lisak, Robert, additional, Jia, Kelly, additional, Mada, Flicia, additional, Bernitsas, Evanthia, additional, Pasnoor, Mamatha, additional, Roath, Katherine, additional, Colgan, Samantha, additional, Currence, Melissa, additional, Heim, Andrew, additional, Barohn, Richard, additional, Dimachkie, Mazen, additional, Statland, Jeffrey, additional, Jawdat, Omar, additional, Jabari, Duaa, additional, Farmakidis, Constantine, additional, Gilchrist, James, additional, Li, Yuebing, additional, Caristo, Irys, additional, Hastings, Debbie, additional, Morren, John Anthony, additional, Weiss, Michael, additional, Muppidi, Srikanth, additional, Nguyen, Tia, additional, Welsh, Lesly, additional, So, Yuen, additional, Goyal, Neelam, additional, Pulley, Michael, additional, Bailey, Cathy, additional, Quraishi, Zubair, additional, Berger, Alan, additional, Sahagian, Gregory, additional, Camberos, Yasmin, additional, and Frishberg, Benjamin, additional
- Published
- 2021
- Full Text
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8. The history of acetylcholinesterase inhibitors in the treatment of myasthenia gravis
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Katz, Natalie K., primary and Barohn, Richard J., additional
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- 2021
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9. NEO1 and NEO-EXT studies: Long-term safety and exploratory efficacy of repeat avalglucosidase alfa dosing for 5.5 years in late-onset Pompe disease patients
- Author
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Dimachkie, Mazen M., primary, Barohn, Richard J., additional, Byrne, Barry, additional, Goker-Alpan, Ozlem, additional, Kishnani, Priya S., additional, Ladha, Shafeeq, additional, Laforêt, Pascal, additional, Mengel, Karl Eugen, additional, Pena, Loren D.M., additional, Sacconi, Sabrina, additional, Straub, Volker, additional, Trivedi, Jaya, additional, Van Damme, Philip, additional, van der Ploeg, Ans, additional, Vissing, John, additional, Young, Peter, additional, Haack, Kristina An, additional, Fleurinck, Carmen, additional, Johnson, Judith, additional, and Liu, Kejian, additional
- Published
- 2020
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10. Long-term effect of thymectomy plus prednisone versus prednisone alone in patients with non-thymomatous myasthenia gravis: 2-year extension of the MGTX randomised trial
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Wolfe, Gil I, primary, Kaminski, Henry J, additional, Aban, Inmaculada B, additional, Minisman, Greg, additional, Kuo, Hui-Chien, additional, Marx, Alexander, additional, Ströbel, Philipp, additional, Mazia, Claudio, additional, Oger, Joel, additional, Cea, J Gabriel, additional, Heckmann, Jeannine M, additional, Evoli, Amelia, additional, Nix, Wilfred, additional, Ciafaloni, Emma, additional, Antonini, Giovanni, additional, Witoonpanich, Rawiphan, additional, King, John O, additional, Beydoun, Said R, additional, Chalk, Colin H, additional, Barboi, Alexandru C, additional, Amato, Anthony A, additional, Shaibani, Aziz I, additional, Katirji, Bashar, additional, Lecky, Bryan R F, additional, Buckley, Camilla, additional, Vincent, Angela, additional, Dias-Tosta, Elza, additional, Yoshikawa, Hiroaki, additional, Waddington-Cruz, Márcia, additional, Pulley, Michael T, additional, Rivner, Michael H, additional, Kostera-Pruszczyk, Anna, additional, Pascuzzi, Robert M, additional, Jackson, Carlayne E, additional, Verschuuren, Jan J G M, additional, Massey, Janice M, additional, Kissel, John T, additional, Werneck, Lineu C, additional, Benatar, Michael, additional, Barohn, Richard J, additional, Tandan, Rup, additional, Mozaffar, Tahseen, additional, Silvestri, Nicholas J, additional, Conwit, Robin, additional, Sonett, Joshua R, additional, Jaretzki, Alfred, additional, Newsom-Davis, John, additional, Cutter, Gary R, additional, Cutter, Gary, additional, Aban, Inmaculada, additional, Feese, Michelle, additional, Wolfe, Gil, additional, Kaminski, Henry, additional, Sonett, Joshua, additional, Saluto, Valeria, additional, Rosenberg, Moises, additional, Alvarez, Valeria, additional, Rey, Lisa, additional, King, John, additional, Butzkueven, Helmut, additional, Goldblatt, John, additional, Carey, John, additional, Pollard, John, additional, Reddel, Stephen, additional, Handel, Nicholas, additional, McCaughan, Brian, additional, Pallot, Linda, additional, Novis, Ricardo, additional, Boasquevisque, Carlos, additional, Morato-Fernandez, Rubens, additional, Ximenes, Manoel, additional, Werneck, Lineu, additional, Scola, Rosana, additional, Soltoski, Paulo, additional, Chalk, Colin, additional, Moore, Fraser, additional, Mulder, David, additional, Wadup, Lisa, additional, Mezei, Michele, additional, Evans, Kenneth, additional, Jiwa, Theresa, additional, Schaffar, Anne, additional, White, Chris, additional, Toth, Cory, additional, Gelfand, Gary, additional, Wood, Susan, additional, Pringle, Elizabeth, additional, Zwicker, Jocelyn, additional, Maziak, Donna, additional, Shamji, Farid, additional, Sundaresan, Sudhir, additional, Seely, Andrew, additional, Cea, Gabriel, additional, Verduga, Renato, additional, Aguayo, Alberto, additional, Jander, Sebastian, additional, Zickler, Philipp, additional, Klein, Michael, additional, Weis, Cleo-Aron, additional, Melms, Arthur, additional, Bischof, Felix, additional, Aebert, Hermann, additional, Ziemer, Gerhard, additional, Thümler, Björn, additional, Wilhem-Schwenkmezger, Thomas, additional, Mayer, Eckhard, additional, Schalke, Berthold, additional, Pöschel, Peter, additional, Hieber, Gisela, additional, Wiebe, Karsten, additional, Clemenzi, Alessandro, additional, Ceschin, Vanessa, additional, Rendina, Erino, additional, Venuta, Federico, additional, Morino, Stefania, additional, Bucci, Elisabetta, additional, Durelli, Luca, additional, Tavella, Alessia, additional, Clerico, Marinella, additional, Contessa, Giulia, additional, Borasio, Piero, additional, Servidei, Serenella, additional, Granone, Pierluigi, additional, Mantegazza, Renato, additional, Berta, Emilia, additional, Novellino, Lorenzo, additional, Spinelli, Luisa, additional, Motomura, Masakatsu, additional, Matsuo, Hidenori, additional, Nagayasu, Takeshi, additional, Takamori, Masaharu, additional, Oda, Makoto, additional, Matsumoto, Isao, additional, Furukawa, Yutaka, additional, Noto, Daisuke, additional, Motozaki, Yuko, additional, Iwasa, Kazuo, additional, Yanase, Daisuke, additional, Garcia Ramos, Guillermo, additional, Cacho, Bernardo, additional, de la Garza, Lorenzo, additional, Kostera-Pruszczyk, Anne, additional, Lipowska, Marta, additional, Kwiecinski, Hubert, additional, Potulska-Chromik, Anna, additional, Orlowski, Tadeusz, additional, Silva, Ana, additional, Feijo, Marta, additional, Freitas, António, additional, Heckmann, Jeannine, additional, Frost, Andrew, additional, Pan, Edward, additional, Tucker, Lawrence, additional, Rossouw, Johan, additional, Drummond, Fiona, additional, Illa, Isabel, additional, Diaz, Jorge, additional, Leon, Carlos, additional, Yeh, Jiann-Horng, additional, Chiu, Hou-Chang, additional, Hsieh, Yei-San, additional, Tunlayadechanont, Supoch, additional, Attanavanich, Sukasom, additional, Verschuuren, Jan, additional, Straathof, Chiara, additional, Titulaer, Maarten, additional, Versteegh, Michel, additional, Pels, Arda, additional, Krum, Yvonne, additional, Leite, M. Isabel, additional, Hilton-Jones, David, additional, Ratnatunga, Chandi, additional, Farrugia, Maria, additional, Petty, Richard, additional, Overell, James, additional, Kirk, Alan, additional, Gibson, Andrew, additional, McDermott, Chris, additional, Hopkinson, David, additional, Lecky, Bryan, additional, Watling, David, additional, Marshall, Dot, additional, Saminaden, Sam, additional, Davies, Deborah, additional, Dougan, Charlotte, additional, Sathasivam, Siva, additional, Page, Richard, additional, Sussman, Jon, additional, Ealing, John, additional, Krysiak, Peter, additional, Amato, Anthony, additional, Salajegheh, Mohammad, additional, Jaklitsch, Michael, additional, Roe, Kristen, additional, Ashizawa, Tetsuo, additional, Smith, Robert Glenn, additional, Zwischenberg, Joseph, additional, Stanton, Penny, additional, Barboi, Alexandru, additional, Jaradeh, Safwan, additional, Tisol, William, additional, Gasparri, Mario, additional, Haasler, George, additional, Yellick, Mary, additional, Dennis, Cedric, additional, Barohn, Richard, additional, Pasnoor, Mamatha, additional, Dimachkie, Mazen, additional, McVey, April, additional, Gronseth, Gary, additional, Dick, Arthur, additional, Kramer, Jeffrey, additional, Currence, Melissa, additional, Herbelin, Laura, additional, Belsh, Jerry, additional, Li, George, additional, Langenfeld, John, additional, Mertz, Mary Ann, additional, Harrison, Taylor, additional, Force, Seth, additional, Usher, Sharon, additional, Beydoun, Said, additional, Lin, Frank, additional, DeMeester, Steve, additional, Akhter, Salem, additional, Malekniazi, Ali, additional, Avenido, Gina, additional, Crum, Brian, additional, Milone, Margherita, additional, Cassivi, Stephen, additional, Fisher, Janet, additional, Heatwole, Chad, additional, Watson, Thomas, additional, Hilbert, James, additional, Smirnow, Alexis, additional, Distad, B. Jane, additional, Weiss, Michael, additional, Wood, Douglas, additional, Haug, Joanna, additional, Ernstoff, Raina, additional, Cao, Jingyang, additional, Chmielewski, Gary, additional, Welsh, Robert, additional, Duris, Robin, additional, Gutmann, Laurie, additional, Pawar, Gauri, additional, Graeber, Geoffrey Marc, additional, Altemus, Patricia, additional, Nance, Christopher, additional, Gutmann, Ludwig, additional, Jackson, Carlayne, additional, Grogan, Patrick, additional, Calhoon, John, additional, Kittrell, Pamela, additional, Myers, Deborah, additional, Hayat, Ghazala, additional, Naunheim, Keith, additional, Eller, Susan, additional, Holzemer, Eve, additional, Alshekhlee, Amer, additional, Robke, Jason, additional, Karlinchak, Brenda, additional, Katz, Jonathan, additional, Miller, Robert, additional, Roan, Ralph, additional, Forshew, Dallas, additional, Kissel, John, additional, Elsheikh, Bakri, additional, Ross, Patrick, additional, Chelnick, Sharon, additional, Lewis, Richard, additional, Acsadi, Agnes, additional, Baciewicz, Frank, additional, Masse, Stacey, additional, Massey, Janice, additional, Juel, Vern, additional, Onaitis, Mark, additional, Lowe, James, additional, Lipscomb, Bernadette, additional, Thai, Gaby, additional, Milliken, Jeffrey, additional, Martin, Veronica, additional, Karayan, Ronnie, additional, Muley, Suraj, additional, Parry, Gareth, additional, Shumway, Sara, additional, Oh, Shin, additional, Claussen, Gwen, additional, Lu, Liang, additional, Cerfolio, Robert, additional, Young, Angela, additional, Morgan, Marla, additional, Pascuzzi, Robert, additional, Kincaid, John, additional, Kesler, Kenneth, additional, Guingrich, Sandy, additional, Michaels, Angi, additional, Phillips, Lawrence, additional, Burns, Ted, additional, Jones, David, additional, Fischer, Cindy, additional, Pulley, Michael, additional, Berger, Alan, additional, D'Agostino, Harry, additional, Smith, Lisa, additional, Rivner, Michael, additional, Pruitt, Jerry, additional, Landolfo, Kevin, additional, Hillman, Demetric, additional, Shaibani, Aziz, additional, Sermas, Angelo, additional, Ruel, Ross, additional, Ismail, Farah, additional, Sivak, Mark, additional, Goldstein, Martin, additional, Camunas, Jorge, additional, Bratton, Joan, additional, Panitch, Hill, additional, Leavitt, Bruce, additional, Jones, Marilee, additional, Muppidi, Srikanth, additional, Vernino, Steven, additional, Nations, Sharon, additional, Meyer, Dan, additional, and Gorham, Nina, additional
- Published
- 2019
- Full Text
- View/download PDF
11. Long-term efficacy and safety of eculizumab in Japanese patients with generalized myasthenia gravis: A subgroup analysis of the REGAIN open-label extension study
- Author
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Murai, Hiroyuki, primary, Uzawa, Akiyuki, additional, Suzuki, Yasushi, additional, Imai, Tomihiro, additional, Shiraishi, Hirokazu, additional, Suzuki, Hidekazu, additional, Okumura, Meinoshin, additional, O’Brien, Fanny, additional, Wang, Jing-Jing, additional, Fujita, Kenji P., additional, Utsugisawa, Kimiaki, additional, Mazia, Claudio Gabriel, additional, Wilken, Miguel, additional, Barroso, Fabio, additional, Saba, Juliet, additional, Rugiero, Marcelo, additional, Bettini, Mariela, additional, Chaves, Marcelo, additional, Vidal, Gonzalo, additional, Garcia, Alejandra Dalila, additional, De Bleecker, Jan, additional, Van den Abeele, Guy, additional, de Koning, Kathy, additional, De Mey, Katrien, additional, Mercelis, Rudy, additional, Mahieu, Délphine, additional, Wagemaekers, Linda, additional, Van Damme, Philip, additional, Depreitere, Annelies, additional, Schotte, Caroline, additional, Smetcoren, Charlotte, additional, Stevens, Olivier, additional, Van Daele, Sien, additional, Vandenbussche, Nicolas, additional, Vanhee, Annelies, additional, Verjans, Sarah, additional, Vynckier, Jan, additional, D'Hondt, Ann, additional, Tilkin, Petra, additional, Alves de Siqueira Carvalho, Alzira, additional, Dias Brockhausen, Igor, additional, Feder, David, additional, Ambrosio, Daniel, additional, César, Pamela, additional, Melo, Ana Paula, additional, Martins Ribeiro, Renata, additional, Rocha, Rosana, additional, Bezerra Rosa, Bruno, additional, Veiga, Thabata, additional, da Silva, Luiz Augusto, additional, Santos Engel, Murilo, additional, Gonçalves Geraldo, Jordana, additional, Ananias Morita, Maria da Penha, additional, Nogueira Coelho, Erica, additional, Paiva, Gabriel, additional, Pozo, Marina, additional, Prando, Natalia, additional, Martineli Torres, Debora Dada, additional, Butinhao, Cristiani Fernanda, additional, Duran, Gustavo, additional, Gomes da Silva, Tamires Cristina, additional, Otavio Maia Gonçalves, Luiz, additional, Pazetto, Lucas Eduardo, additional, Fialho, Tomás Augusto Suriane, additional, Renata Cubas Volpe, Luciana, additional, Souza Duca, Luciana, additional, Souza Bulle Oliveira, Acary, additional, Amaral Andrade, Ana Carolina, additional, Annes, Marcelo, additional, Duarte Silva, Liene, additional, Cavalcante Lino, Valeria, additional, Pinto, Wladimir, additional, Assis, Natália, additional, Carrara, Fernanda, additional, Miranda, Carolina, additional, Souza, Iandra, additional, Fernandes, Patricia, additional, Siddiqi, Zaeem, additional, Phan, Cecile, additional, Narayan, Jeffrey, additional, Blackmore, Derrick, additional, Mallon, Ashley, additional, Roderus, Rikki, additional, Watt, Elizabeth, additional, Junkerova, Jana, additional, Kurkova, Barbora, additional, Reguliova, Katarina, additional, Zapletalova, Olga, additional, Pitha, Jiri, additional, Novakova, Iveta, additional, Tyblova, Michaela, additional, Jurajdova, Ivana, additional, Wolfova, Marcela, additional, Andersen, Henning, additional, Harbo, Thomas, additional, Vinge, Lotte, additional, Krogh, Susanne, additional, Mogensen, Anita, additional, Vissing, John, additional, Højgaard, Joan, additional, Witting, Nanna, additional, Mette Ostergaard Autzen, Anne, additional, Pedersen, Jane, additional, Eralinna, Juha-Pekka, additional, Laaksonen, Mikko, additional, Oksaranta, Olli, additional, Harrison, Tuula, additional, Eriksson, Jaana, additional, Rozsa, Csilla, additional, Horvath, Melinda, additional, Lovas, Gabor, additional, Matolcsi, Judit, additional, Szabo, Gyorgyi, additional, Jakab, Gedeonne, additional, Szabadosne, Brigitta, additional, Antonini, Giovanni, additional, Di Pasquale, Antonella, additional, Garibaldi, Matteo, additional, Morino, Stefania, additional, Troili, Fernanda, additional, Fionda, Laura, additional, Filla, Allessandro, additional, Costabile, Teresa, additional, Marano, Enrico, additional, Saccà, Francesco, additional, Fasanaro, Angiola, additional, Marsili, Angela, additional, Puorro, Giorgia, additional, Mantegazza, Renato, additional, Antozzi, Carlo, additional, Bonanno, Silvia, additional, Camera, Giorgia, additional, Locatelli, Alberta, additional, Maggi, Lorenzo, additional, Pasanisi, Maria, additional, Campanella, Angela, additional, Evoli, Amelia, additional, Alboini, Paolo Emilio, additional, D'Amato, Valentina, additional, Iorio, Raffaele, additional, Kanai, Tetsuya, additional, Kawaguchi, Naoki, additional, Mori, Masahiro, additional, Kaneko, Yoko, additional, Kanzaki, Akiko, additional, Kobayashi, Eri, additional, Masaki, Katsuhisa, additional, Matsuse, Dai, additional, Matsushita, Takuya, additional, Uehara, Taira, additional, Shimpo, Misa, additional, Jingu, Maki, additional, Kikutake, Keiko, additional, Nakamura, Yumiko, additional, Sano, Yoshiko, additional, Nagane, Yuriko, additional, Kamegamori, Ikuko, additional, Tsuda, Tomoko, additional, Fujii, Yuko, additional, Futono, Kazumi, additional, Ozawa, Yukiko, additional, Mizugami, Aya, additional, Saito, Yuka, additional, Morikawa, Miyuki, additional, Samukawa, Makoto, additional, Kamakura, Sachiko, additional, Miyawaki, Eriko, additional, Mitazaki, Teiichiro, additional, Motomura, Masakatsu, additional, Mukaino, Akihiro, additional, Yoshimura, Shunsuke, additional, Asada, Shizuka, additional, Yoshida, Seiko, additional, Amamoto, Shoko, additional, Kobashikawa, Tomomi, additional, Koga, Megumi, additional, Maeda, Yasuko, additional, Takada, Kazumi, additional, Takada, Mihoko, additional, Tsurumaru, Masako, additional, Yamashita, Yumi, additional, Akiyama, Tetsuya, additional, Narikawa, Koichi, additional, Tano, Ohito, additional, Tsukita, Kenichi, additional, Kurihara, Rikako, additional, Meguro, Fumie, additional, Fukuda, Yusuke, additional, Sato, Miwako, additional, Funaka, Soichiro, additional, Kawamura, Tomohiro, additional, Makamori, Masayuki, additional, Takahashi, Masanori, additional, Taichi, Namie, additional, Hasuike, Tomoya, additional, Higuchi, Eriko, additional, Kobayashi, Hisako, additional, Osakada, Kaori, additional, Tsuda, Emiko, additional, Shimohama, Shun, additional, Hayashi, Takashi, additional, Hisahara, Shin, additional, Kawamata, Jun, additional, Murahara, Takashi, additional, Saitoh, Masaki, additional, Suzuki, Shuichiro, additional, Yamamoto, Daisuke, additional, Ishiyama, Yoko, additional, Ishiyama, Naoko, additional, Noshiro, Mayuko, additional, Takeyama, Rumi, additional, Uwasa, Kaori, additional, Yasuda, Ikuko, additional, van der Kooi, Anneke, additional, de Visser, Marianne, additional, Gibson, Tamar, additional, Casasnovas, Carlos, additional, Alberti Aguilo, Maria Antonia, additional, Homedes-Pedret, Christian, additional, Julia Palacios, Natalia, additional, Diez Porras, Laura, additional, Velez Santamaria, Valentina, additional, Lazaro, Ana, additional, Diez Tejedor, Exuperio, additional, Gomez Salcedo, Pilar, additional, Fernandez-Fournier, Mireya, additional, Lopez Ruiz, Pedro, additional, Rodriguez de Rivera, Francisco Javier, additional, Sastre, Maria, additional, Gamez, Josep, additional, Sune, Pilar, additional, Salvado, Maria, additional, Gili, Gisela, additional, Mazuela, Gonzalo, additional, Illa, Isabel, additional, Cortes Vicente, Elena, additional, Diaz-Manera, Jordi, additional, Querol Gutierrez, Luis Antonio, additional, Rojas Garcia, Ricardo, additional, Vidal, Nuria, additional, Arribas-Ibar, Elisabet, additional, Piehl, Fredrik, additional, Hietala, Albert, additional, Bjarbo, Lena, additional, Sengun, Ihsan, additional, Meherremova, Arzu, additional, Ozcelik, Pinar, additional, Balkan, Bengu, additional, Tuga, Celal, additional, Ugur, Muzeyyen, additional, Erdem-Ozdamar, Sevim, additional, Bekircan-Kurt, Can Ebru, additional, Acar, Nazire Pinar, additional, Yilmaz, Ezgi, additional, Caliskan, Yagmur, additional, Orsel, Gulsah, additional, Efendi, Husnu, additional, Aydinlik, Seda, additional, Cavus, Hakan, additional, Kutlu, Ayse, additional, Becerikli, Gulsah, additional, Semiz, Cansu, additional, Tun, Ozlem, additional, Terzi, Murat, additional, Dogan, Baki, additional, Onar, Musa Kazim, additional, Sen, Sedat, additional, Kirbas Cavdar, Tugce, additional, Veske, Adife, additional, Norwood, Fiona, additional, Dimitriou, Aikaterini, additional, Gollogly, Jakit, additional, Mahdi-Rogers, Mohamed, additional, Seddigh, Arshira, additional, Sokratous, Giannis, additional, Maier, Gal, additional, Sohail, Faisal, additional, Jacob, Saiju, additional, Sadalage, Girija, additional, Torane, Pravin, additional, Brown, Claire, additional, Shah, Amna, additional, Sathasivam, Sivakumar, additional, Arndt, Heike, additional, Davies, Debbie, additional, Watling, Dave, additional, Amato, Anthony, additional, Cochrane, Thomas, additional, Salajegheh, Mohammed, additional, Roe, Kristen, additional, Amato, Katherine, additional, Toska, Shirli, additional, Wolfe, Gil, additional, Silvestri, Nicholas, additional, Patrick, Kara, additional, Zakalik, Karen, additional, Katz, Jonathan, additional, Miller, Robert, additional, Engel, Marguerite, additional, Forshew, Dallas, additional, Bravver, Elena, additional, Brooks, Benjamin, additional, Plevka, Sarah, additional, Burdette, Maryanne, additional, Cunningham, Scott, additional, Sanjak, Mohammad, additional, Kramer, Megan, additional, Nemeth, Joanne, additional, Schommer, Clara, additional, Tierney, Scott, additional, Juel, Vern, additional, Guptill, Jeffrey, additional, Hobson-Webb, Lisa, additional, Massey, Janice, additional, Beck, Kate, additional, Carnes, Donna, additional, Loor, John, additional, Anderson, Amanda, additional, Pascuzzi, Robert, additional, Bodkin, Cynthia, additional, Kincaid, John, additional, Snook, Riley, additional, Guingrich, Sandra, additional, Micheels, Angela, additional, Chaudhry, Vinay, additional, Corse, Andrea, additional, Mosmiller, Betsy, additional, Kelley, Andrea, additional, Ho, Doreen, additional, Srinivasan, Jayashri, additional, Vytopil, Michal, additional, Jara, Jordan, additional, Ventura, Nicholas, additional, Scala, Stephanie, additional, Carter, Cynthia, additional, Donahue, Craig, additional, Herbert, Carol, additional, Weiner, Elaine, additional, Alam, Sharmeen, additional, McKinnon, Jonathan, additional, Haar, Laura, additional, McKinnon, Naya, additional, Alcon, Karan, additional, McKenna, Kaitlyn, additional, Sattar, Nadia, additional, Daniels, Kevin, additional, Jeffery, Dennis, additional, Freimer, Miriam, additional, Hoyle, Joseph Chad, additional, Kissel, John, additional, Agriesti, Julie, additional, Chelnick, Sharon, additional, Mezache, Louisa, additional, Pineda, Colleen, additional, Muharrem, Filiz, additional, Karam, Chafic, additional, Khoury, Julie, additional, Marburger, Tessa, additional, Kaur, Harpreet, additional, Dimitrova, Diana, additional, Gilchrist, James, additional, Agrawal, Brajesh, additional, Elsayed, Mona, additional, Kohlrus, Stephanie, additional, Andoin, Angela, additional, Darnell, Taylor, additional, Golden, Laura, additional, Lokaitis, Barbara, additional, Seelback, Jenna, additional, Muppidi, Srikanth, additional, Goyal, Neelam, additional, Sakamuri, Sarada, additional, So, Yuen T., additional, Paulose, Shirley, additional, Pol, Sabrina, additional, Welsh, Lesly, additional, Bhavaraju-Sanka, Ratna, additional, Tobon Gonzales, Alejandro, additional, Dishman, Lorraine, additional, Jones, Floyd, additional, Gonzalez, Anna, additional, Padilla, Patricia, additional, Saklad, Amy, additional, Silva, Marcela, additional, Kazamel, Mohamed, additional, Alsharabati, Mohammad, additional, Lu, Liang, additional, Nozaki, Kenkichi, additional, Mumfrey-Thomas, Sandi, additional, Woodall, Amy, additional, Mozaffar, Tahseen, additional, Cash, Tiyonnoh, additional, Goyal, Namita, additional, Roy, Gulmohor, additional, Mathew, Veena, additional, Maqsood, Fatima, additional, Minton, Brian, additional, Jones, H. James, additional, Rosenfeld, Jeffrey, additional, Garcia, Rebekah, additional, Echevarria, Laura, additional, Garcia, Sonia, additional, Pulley, Michael, additional, Aranke, Shachie, additional, Berger, Alan Ross, additional, Shah, Jaimin, additional, Shabbir, Yasmeen, additional, Smith, Lisa, additional, Varghese, Mary, additional, Gutmann, Laurie, additional, Gutmann, Ludwig, additional, Jerath, Nivedita, additional, Nance, Christopher, additional, Swenson, Andrea, additional, Olalde, Heena, additional, Kressin, Nicole, additional, Sieren, Jeri, additional, Barohn, Richard, additional, Dimachkie, Mazen, additional, Glenn, Melanie, additional, McVey, April, additional, Pasnoor, Mamatha, additional, Statland, Jeffery, additional, Wang, Yunxia, additional, Liu, Tina, additional, Emmons, Kelley, additional, Jenci, Nicole, additional, Locheke, Jerry, additional, Fondaw, Alex, additional, Johns, Kathryn, additional, Rico, Gabrielle, additional, Walsh, Maureen, additional, Herbelin, Laura, additional, Hafer-Macko, Charlene, additional, Kwan, Justin, additional, Zilliox, Lindsay, additional, Callison, Karen, additional, Young, Valerie, additional, DiSanzo, Beth, additional, Naunton, Kerry, additional, Benatar, Michael, additional, Bilsker, Martin, additional, Sharma, Khema, additional, Cooley, Anne, additional, Reyes, Eliana, additional, Michon, Sara-Claude, additional, Sheldon, Danielle, additional, Steele, Julie, additional, Howard Jr, James, additional, Chopra, Manisha, additional, Traub, Rebecca, additional, Vu, Tuan, additional, Katzin, Lara, additional, McClain, Terry, additional, Harvey, Brittany, additional, Hart, Adam, additional, Huynh, Kristin, additional, Beydoun, Said, additional, Chilingaryan, Amaiak, additional, Doan, Victor, additional, Droker, Brian, additional, Gong, Hui, additional, Karimi, Sanaz, additional, Lin, Frank, additional, Pokala, Krishna, additional, Shah, Akshay, additional, Tran, Anh, additional, Akhter, Salma, additional, Malekniazi, Ali, additional, Tandan, Rup, additional, Hehir, Michael, additional, Waheed, Waqar, additional, Lucy, Shannon, additional, Weiss, Michael, additional, Distad, Jane, additional, Strom, Susan, additional, Downing, Sharon, additional, Kim, Bryan, additional, Nowak, Richard, additional, Dicapua, Daniel, additional, Keung, Benison, additional, Kumar, Aditya, additional, Patwa, Huned, additional, Robeson, Kimberly, additional, Yang, Irene, additional, Nye, Joan, additional, and Vu, Hong, additional
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- 2019
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12. Safety and efficacy of intravenous bimagrumab in inclusion body myositis (RESILIENT): a randomised, double-blind, placebo-controlled phase 2b trial
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Hanna, Michael G, primary, Badrising, Umesh A, additional, Benveniste, Olivier, additional, Lloyd, Thomas E, additional, Needham, Merrilee, additional, Chinoy, Hector, additional, Aoki, Masashi, additional, Machado, Pedro M, additional, Liang, Christina, additional, Reardon, Katrina A, additional, de Visser, Marianne, additional, Ascherman, Dana P, additional, Barohn, Richard J, additional, Dimachkie, Mazen M, additional, Miller, James A L, additional, Kissel, John T, additional, Oskarsson, Björn, additional, Joyce, Nanette C, additional, Van den Bergh, Peter, additional, Baets, Jonathan, additional, De Bleecker, Jan L, additional, Karam, Chafic, additional, David, William S, additional, Mirabella, Massimiliano, additional, Nations, Sharon P, additional, Jung, Hans H, additional, Pegoraro, Elena, additional, Maggi, Lorenzo, additional, Rodolico, Carmelo, additional, Filosto, Massimiliano, additional, Shaibani, Aziz I, additional, Sivakumar, Kumaraswamy, additional, Goyal, Namita A, additional, Mori-Yoshimura, Madoka, additional, Yamashita, Satoshi, additional, Suzuki, Naoki, additional, Katsuno, Masahisa, additional, Murata, Kenya, additional, Nodera, Hiroyuki, additional, Nishino, Ichizo, additional, Romano, Carla D, additional, Williams, Valerie S L, additional, Vissing, John, additional, Auberson, Lixin Zhang, additional, Wu, Min, additional, de Vera, Ana, additional, Papanicolaou, Dimitris A, additional, and Amato, Anthony A, additional
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- 2019
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13. Safety, tolerability, pharmacokinetics, pharmacodynamics, and exploratory efficacy of the novel enzyme replacement therapy avalglucosidase alfa (neoGAA) in treatment-naïve and alglucosidase alfa-treated patients with late-onset Pompe disease: A phase 1, open-label, multicenter, multinational, ascending dose study
- Author
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Pena, Loren D.M., primary, Barohn, Richard J., additional, Byrne, Barry J., additional, Desnuelle, Claude, additional, Goker-Alpan, Ozlem, additional, Ladha, Shafeeq, additional, Laforêt, Pascal, additional, Mengel, Karl Eugen, additional, Pestronk, Alan, additional, Pouget, Jean, additional, Schoser, Benedikt, additional, Straub, Volker, additional, Trivedi, Jaya, additional, Van Damme, Philip, additional, Vissing, John, additional, Young, Peter, additional, Kacena, Katherine, additional, Shafi, Raheel, additional, Thurberg, Beth L., additional, Culm-Merdek, Kerry, additional, and van der Ploeg, Ans T., additional
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- 2019
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14. Progress in Drug Discovery in Academia and Persistent Challenges of “the Valley of Death”
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Barohn, Richard J., primary, Weir, Scott J., additional, and Simari, Robert D., additional
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- 2019
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15. NEO1 and NEO-EXT studies: Long-term safety of repeat avalglucosidase alfa dosing for 4.5 years in late-onset Pompe disease patients
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Pena, Loren, primary, Barohn, Richard J., additional, Dimachkie, Mazen M., additional, Kishnani, Priya S., additional, Ladha, Shafeeq, additional, Mengel, Karl-Eugen, additional, Sacconi, Sabrina, additional, Van Damme, Philip, additional, Vissing, John, additional, Haack, Kristina An, additional, Hug, Christopher, additional, Johnson, Judith, additional, Sensinger, Charlotte, additional, and Schoser, Benedikt, additional
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- 2019
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16. Intravenous versus subcutaneous immunoglobulin – Authors' reply
- Author
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van Schaik, Ivo N, primary, Mielke, Orell, additional, Sabet, Arman, additional, George, Koshy, additional, Roberts, Leslie, additional, Carne, Ross, additional, Blum, Stefan, additional, Henderson, Robert, additional, Van Damme, Philip, additional, Demeestere, Jelle, additional, Larue, Sandrine, additional, Pinard D'Amour, Catherine-Andree, additional, Bril, Vera, additional, Breiner, Ari, additional, Kunc, Pavel, additional, Valis, Martin, additional, Sussova, Jana, additional, Kalous, Tomas, additional, Talab, Radomir, additional, Bednar, Michal, additional, Toomsoo, Toomas, additional, Rubanovits, Inna, additional, Gross-Paju, Katrin, additional, Sorro, Ulvi, additional, Saarela, Mika, additional, Auranen, Mari, additional, Pouget, Jean, additional, Attarian, Shahram, additional, Le Masson, Gwendal, additional, Wielanek-Bachelet, Anne-Cécile, additional, Desnuelle, Claude, additional, Delmont, Emilien, additional, Clavelou, Pierre, additional, Aufauvre, Dominique, additional, Schmidt, Jens, additional, Zschuentssch, Jana, additional, Sommer, Claudia, additional, Kramer, Daniela, additional, Hoffmann, Olaf, additional, Goerlitz, Carsten, additional, Haas, Judith, additional, Chatzopoulos, Marko, additional, Yoon, Min-Suk, additional, Gold, Ralf, additional, Berlit, Peter, additional, Jaspert-Grehl, Andrea, additional, Liebetanz, David, additional, Kutschenko, Anna, additional, Stangel, Martin, additional, Trebst, Corinna, additional, Baum, Petra, additional, Then Bergh, Florian, additional, Klehmet, Juliane, additional, Meisel, Andreas, additional, Klostermann, Fabian, additional, Oechtering, Johanna, additional, Lehmann, Helmar, additional, Schroeter, Michael, additional, Hagenacker, Tim, additional, Mueller, Daniel, additional, Sperfeld, Anne-Dorte, additional, Bethke, Florian, additional, Hartung, Hans-Peter, additional, Drory, Vivian, additional, Algom, Avi, additional, Yarnitsky, David, additional, Murinson, Beth Brianna, additional, Di Muzio, Antonio, additional, Ciccocioppo, Fausta, additional, Sorbi, Sandro, additional, Mata, Sabrina, additional, Schenone, Angelo, additional, Grandis, Marina, additional, Lauria, Giuseppe, additional, Cazzato, Daniele, additional, Antonini, Giovanni, additional, Morino, Stefania, additional, Cocito, Dario, additional, Zibetti, Maurizio, additional, Yokota, Takanori, additional, Ohkubo, Takuya, additional, Kanda, Takashi, additional, Kawai, Motoharu, additional, Kaida, Kenichi, additional, Onoue, Hiroyuki, additional, Kuwabara, Satoshi, additional, Mori, Masahiro, additional, Iijima, Masahiro, additional, Ohyama, Ken, additional, Sobue, Gen, additional, Baba, Masayuki, additional, Tomiyama, Masahiko, additional, Nishiyama, Kazutoshi, additional, Akutsu, Tsugio, additional, Yokoyama, Kazumasa, additional, Kanai, Kazuaki, additional, van Schaik, Ivo N., additional, Eftimov, Filip, additional, Notermans, Nicolette. C., additional, Visser, Nora. A., additional, Faber, Catharina, additional, Hoeijmakers, Janneke. G.J., additional, Merkies, Ingemar S.J., additional, van Geloven, Nan, additional, Rejdak, Konrad, additional, Chyrchel-Paszkiewicz, Urszula, additional, Casanovas Pons, Carlos, additional, Alberti Aguiló, María Antonia, additional, Gamez, Josep, additional, Figueras, María, additional, Marquez Infante, Celedonio, additional, Benitez Rivero, Sonia, additional, Lunn, Michael, additional, Morrow, Jasper, additional, Gosal, David, additional, Lavin, Timothy Myles, additional, Melamed, Isaac, additional, Testori, Alessandro, additional, Ajroud-Driss, Senda, additional, Menichella, Daniela, additional, Simpson, Ericka, additional, Chi-Ho Lai, Eugene, additional, Dimachkie, Mazen, additional, Barohn, Richard J., additional, Beydoun, Said, additional, Johl, Harpreet, additional, Lange, Dale, additional, Shtilbans, Alexander, additional, Muley, Suraj, additional, Ladha, Shafeeq, additional, Freimer, Miriam, additional, Kissel, John, additional, Latov, Norman, additional, Chin, Russell, additional, Ubogu, Eroboghene, additional, Mumfrey, Sandi, additional, Rao, T. Hermanth P., additional, MacDonald, Paul, additional, Sharma, Khema, additional, Gonzalez, Ginna, additional, Allen, Jeffrey, additional, Walk, David, additional, Hobson-Webb, Lisa, additional, Gable, Karissa, additional, Lewis, Richard A., additional, Cornblath, David R., additional, Lawo, John-Phillip, additional, Praus, Michaela, additional, and Durn, Billie L., additional
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- 2018
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17. Neuromuscular Junction Disorders
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Dimachkie, Mazen M., primary and Barohn, Richard J., additional
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- 2018
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18. Diagnosis of Myasthenia Gravis
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Pasnoor, Mamatha, primary, Dimachkie, Mazen M., additional, Farmakidis, Constantine, additional, and Barohn, Richard J., additional
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- 2018
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19. Fifty Key Publications on Myasthenia Gravis and Related Disorders
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Dimachkie, Mazen M., primary and Barohn, Richard J., additional
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- 2018
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20. Treatment of Myasthenia Gravis
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Farmakidis, Constantine, primary, Pasnoor, Mamatha, additional, Dimachkie, Mazen M., additional, and Barohn, Richard J., additional
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- 2018
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21. Muscle-Specific Tyrosine Kinase and Myasthenia Gravis Owing to Other Antibodies
- Author
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Rivner, Michael H., primary, Pasnoor, Mamatha, additional, Dimachkie, Mazen M., additional, Barohn, Richard J., additional, and Mei, Lin, additional
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- 2018
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22. Measuring Clinical Treatment Response in Myasthenia Gravis
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Barnett, Carolina, primary, Herbelin, Laura, additional, Dimachkie, Mazen M., additional, and Barohn, Richard J., additional
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- 2018
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23. Lambert-Eaton Myasthenic Syndrome
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Kesner, Vita G., primary, Oh, Shin J., additional, Dimachkie, Mazen M., additional, and Barohn, Richard J., additional
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- 2018
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24. Safety and efficacy of eculizumab in anti-acetylcholine receptor antibody-positive refractory generalised myasthenia gravis (REGAIN): a phase 3, randomised, double-blind, placebo-controlled, multicentre study
- Author
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Howard, James F, primary, Utsugisawa, Kimiaki, additional, Benatar, Michael, additional, Murai, Hiroyuki, additional, Barohn, Richard J, additional, Illa, Isabel, additional, Jacob, Saiju, additional, Vissing, John, additional, Burns, Ted M, additional, Kissel, John T, additional, Muppidi, Srikanth, additional, Nowak, Richard J, additional, O'Brien, Fanny, additional, Wang, Jing-Jing, additional, Mantegazza, Renato, additional, Mazia, Claudio Gabriel, additional, Wilken, Miguel, additional, Ortea, Carolina, additional, Saba, Juliet, additional, Rugiero, Marcelo, additional, Bettini, Mariela, additional, Vidal, Gonzalo, additional, Garcia, Alejandra Dalila, additional, Lamont, Phillipa, additional, Leong, Wai-Kuen, additional, Boterhoven, Heidi, additional, Fyfe, Beverly, additional, Roberts, Leslie, additional, Jasinarachchi, Mahi, additional, Willlems, Natasha, additional, Wanschitz, Julia, additional, Löscher, Wolfgang, additional, De Bleecker, Jan, additional, Van den Abeele, Guy, additional, de Koning, Kathy, additional, De Mey, Katrien, additional, Mercelis, Rudy, additional, Wagemaekers, Linda, additional, Mahieu, Delphine, additional, Van Damme, Philip, additional, Smetcoren, Charlotte, additional, Stevens, Olivier, additional, Verjans, Sarah, additional, D'Hondt, Ann, additional, Tilkin, Petra, additional, Alves de Siqueira Carvalho, Alzira, additional, Hasan, Rosa, additional, Dias Brockhausen, Igor, additional, Feder, David, additional, Ambrosio, Daniel, additional, Melo, Ana Paula, additional, Rocha, Rosana, additional, Rosa, Bruno, additional, Veiga, Thabata, additional, Augusto da Silva, Luiz, additional, Gonçalves Geraldo, Jordana, additional, da Penha Morita Ananias, Maria, additional, Nogueira Coelho, Erica, additional, Paiva, Gabriel, additional, Pozo, Marina, additional, Prando, Natalia, additional, Dada Martineli Torres, Debora, additional, Fernanda Butinhao, Cristiani, additional, Coelho, Erica, additional, Renata Cubas Volpe, Luciana, additional, Duran, Gustavo, additional, Gomes da Silva, Tamires Cristina, additional, Otavio Maia Gonçalves, Luiz, additional, Pazetto, Lucas Eduardo, additional, Souza Duca, Luciana, additional, Suriane Fialho, Tomás Augusto, additional, Gheller Friedrich, Maurício André, additional, Guerreiro, Alexandre, additional, Mohr, Henrique, additional, Pereira Martins, Maurer, additional, da Cruz Pacheco, Daiane, additional, Macagnan, Ana Paula, additional, de Cassia Santos, Aline, additional, Bulle Oliveira, Acary Souza, additional, Amaral de Andrade, Ana Carolina, additional, Annes, Marcelo, additional, Cavalcante Lino, Valeria, additional, Pinto, Wladimir, additional, Miranda, Carolina, additional, Carrara, Fernanda, additional, Souza, Iandra, additional, Genge, Angela, additional, Massie, Rami, additional, Campbell, Natasha, additional, Bril, Vera, additional, Katzberg, Hans, additional, Soltani, Mehran, additional, Ng, Eduardo, additional, Siddiqi, Zaeem, additional, Phan, Celile, additional, Blackmore, Derrick, additional, Vohanka, Stanislav, additional, Bednarik, Josef, additional, Chmelikova, Magda, additional, Cierny, Marek, additional, Toncrova, Stanislava, additional, Junkerova, Jana, additional, Kurkova, Barbora, additional, Reguliova, Katarina, additional, Zapletalova, Olga, additional, Pitha, Jiri, additional, Novakova, Iveta, additional, Tyblova, Michaela, additional, Wolfova, Marcela, additional, Jurajdova, Ivana, additional, Andersen, Henning, additional, Harbo, Thomas, additional, Vinge, Lotte, additional, Mogensen, Anita, additional, Højgaard, Joan, additional, Witting, Nanna, additional, Autzen, Anne Mette, additional, Pedersen, Jane, additional, Färkkilä, Markus, additional, Atula, Sari, additional, Nyrhinen, Anne, additional, Erälinna, Juha-Pekka, additional, Laaksonen, Mikko, additional, Oksaranta, Olli, additional, Eriksson, Jaana, additional, Harrison, Tuula, additional, Desnuelle, Claude, additional, Sacconi, Sabrina, additional, Soriani, Marie-Hélène, additional, Decressac, Sonia, additional, Moutarde, Julie, additional, Lahaut, Pauline, additional, Solé, Guilhem, additional, Le Masson, Gwendal, additional, Wielanek-Bachelet, Anne-Cécile, additional, Gaboreau, Morgane, additional, Moreau, Caroline, additional, Wilson, Amy, additional, Vial, Christophe, additional, Bouhour, Françoise, additional, Gervais-Bernard, Helene, additional, Merle, Hélène, additional, Hourquin, Caroline, additional, Lacour, Arnaud, additional, Outteryck, Olivier, additional, Vermersch, Patrick, additional, Zephir, Hélène, additional, Millois, Edouard, additional, Deneve, Michel, additional, Deruelle, Fabienne, additional, Schoser, Benedikt, additional, Wenninger, Stephan, additional, Stangel, Martin, additional, Alvermann, Sascha, additional, Gingele, Stefan, additional, Skripuletz, Thomas, additional, Suehs, Kurt-Wolfram, additional, Trebst, Corinna, additional, Fricke, Karin, additional, Papagiannopoulos, Sotirios, additional, Bostantzopoulou, Sevasti, additional, Vlaikidis, Nicholas, additional, Zampaki, Martha, additional, Papadopoulou, Nikoletta, additional, Mitsikostas, Dimos-Dimitrios, additional, Kasioti, Eleni, additional, Mitropoulou, Efstathia, additional, Charalambous, Despoina, additional, Rozsa, Csilla, additional, Horvath, Melinda, additional, Lovas, Gabor, additional, Matolcsi, Judit, additional, Szabo, Gyorgyi, additional, Szabadosne, Brigitta, additional, Vecsei, Laszlo, additional, Dezsi, Livia, additional, Varga, Edina, additional, Konyane, Monika, additional, Gross, Bella, additional, Azrilin, Olga, additional, Greenbereg, Nelly, additional, Bali Kuperman, Hila, additional, Antonini, Giovanni, additional, Garibaldi, Matteo, additional, Morino, Stefania, additional, Troili, Fernanda, additional, Di Pasquale, Antonella, additional, Filla, Alessandro, additional, Costabile, Teresa, additional, Marano, Enrico, additional, Sacca, Francesco, additional, Marsil, Angela, additional, Puorro, Giorgia, additional, Maestri Tassoni, Michelangelo, additional, De Rosa, Anna, additional, Bonanno, Silvia, additional, Antozzi, Carlo, additional, Maggi, Lorenzo, additional, Campanella, Angela, additional, Angelini, Corrado, additional, Cudia, Paola, additional, Pegoraro, Valentina, additional, Pinzan, Elena, additional, Bevilacqua, Francesca, additional, Orrico, Daniele, additional, Bonifati, Domenico Marco, additional, Evoli, Amelia, additional, Alboini, Paolo Emilio, additional, D'Amato, Valentina, additional, Iorio, Raffaele, additional, Inghilleri, Maurizio, additional, Fionda, Laura, additional, Frasca, Vittorio, additional, Giacomelli, Elena, additional, Gori, Maria, additional, Lopergolo, Diego, additional, Onesti, Emanuela, additional, Gabriele, Maria, additional, Patti, Francesco, additional, Salvatore Caramma, Andrea, additional, Messina, Silvia, additional, Reggio, Ester, additional, Caserta, Cinzia, additional, Uzawa, Akiyuki, additional, Kanai, Tetsuya, additional, Mori, Masahiro, additional, Kaneko, Yoko, additional, Kanzaki, Akiko, additional, Kobayashi, Eri, additional, Masaki, Katsuhisa, additional, Matsuse, Dai, additional, Matsushita, Takuya, additional, Uehara, Taira, additional, Shimpo, Misa, additional, Jingu, Maki, additional, Kikutake, Keiko, additional, Nakamura, Yumiko, additional, Sano, Yoshiko, additional, Nagane, Yuriko, additional, Kamegamori, Ikuko, additional, Fujii, Yuko, additional, Futono, Kazumi, additional, Tsuda, Tomoko, additional, Saito, Yuka, additional, Suzuki, Hidekazu, additional, Morikawa, Miyuki, additional, Samukawa, Makoto, additional, Kamakura, Sachiko, additional, Shiraishi, Hirokazu, additional, Mitazaki, Teiichiro, additional, Motomura, Masakatsu, additional, Mukaino, Akihiro, additional, Yoshimura, Shunsuke, additional, Asada, Shizuka, additional, Kobashikawa, Tomomi, additional, Koga, Megumi, additional, Maeda, Yasuko, additional, Takada, Kazumi, additional, Takada, Mihoko Takada, additional, Yamashita, Yumi, additional, Yoshida, Seiko, additional, Suzuki, Yasushi, additional, Akiyama, Tetsuya, additional, Narikawa, Koichi, additional, Tsukita, Kenichi, additional, Meguro, Fumie, additional, Fukuda, Yusuke, additional, Sato, Miwako, additional, Matsuo, Hidenori, additional, Fukudome, Takayasu, additional, Gondo, Yuichiro, additional, Maeda, Yasuhiro, additional, Nagaishi, Akiko, additional, Nakane, Shunya, additional, Okubo, Yoshinori, additional, Okumura, Meinoshin, additional, Funaka, Soichiro, additional, Kawamura, Tomohiro, additional, Makamori, Masayuki, additional, Takahashi, Masanori, additional, Hasuike, Tomoya, additional, Higuchi, Eriko, additional, Kobayashi, Hisako, additional, Osakada, Kaori, additional, Taichi, Namie, additional, Tsuda, Emiko, additional, Hayashi, Takashi, additional, Hisahara, Shin, additional, Imai, Tomihiro, additional, Kawamata, Jun, additional, Murahara, Takashi, additional, Saitoh, Masaki, additional, Shimohama, Shun, additional, Suzuki, Shuichiro, additional, Yamamoto, Daisuke, additional, Konno, Shingo, additional, Imamura, Tomomi, additional, Inoue, Masashi, additional, Murata, Mayumi, additional, Nakazora, Hiroshi, additional, Nakayama, Ritsu, additional, Ikeda, Yasuko, additional, Ogawa, Miki, additional, Shirane, Maoko, additional, Kanda, Takashi, additional, Kawai, Motoharu, additional, Koga, Michiaki, additional, Ogasawara, Junichi, additional, Omoto, Masatoshi, additional, Sano, Yasuteru, additional, Arima, Hideki, additional, Fukui, Sachie, additional, Shimose, Shigemi, additional, Shinozaki, Hirokazu, additional, Watanabe, Masanori, additional, Yoshikawa, Chieko, additional, van der Kooi, Anneke, additional, de Visser, Marianne, additional, Gibson, Tamar, additional, Maessen, Jos, additional, de Baets, Marc, additional, Faber, Catherine, additional, Keijzers, Maria Johanna, additional, Miesen, Monique, additional, Kostera-Pruszczyk, Anna, additional, Kaminska, Anna, additional, Kim, Byung-Jo, additional, Lee, Chang Nyoung, additional, Koo, Yong Seo, additional, Seok, Hung Youl, additional, Kang, Hoo Nam, additional, Ra, HyeJin, additional, Kim, Byoung Joon, additional, Cho, Eun Bin, additional, Lee, HyeLim, additional, Min, Ju-Hong, additional, Seok, Jinmyoung, additional, Koh, Da Yoon, additional, Kwon, JuYoung, additional, Lee, JiEun, additional, Park, SangAe, additional, Hong, Yoon-Ho, additional, Lim, Jae-Sung, additional, Kim, MiRi, additional, Kim, Seung Min, additional, Kim, Yool-hee, additional, Lee, Hyung Seok, additional, Shin, Ha Young, additional, Hwang, Eun Bi, additional, Shin, MiJu, additional, Sazonov, Denis, additional, Yarmoschuk, Asya, additional, Babenko, Larisa, additional, Malkova, Nadezhda, additional, Melnikova, Anna, additional, Korobko, Denis, additional, Kosykh, Evgeniya, additional, Pokhabov, Dmitry, additional, Nesterova, Yulia, additional, Abramov, Vladislav, additional, Balyazin, Victor, additional, Casasnovas Pons, Carlos, additional, Alberti Aguilo, Maria, additional, Homedes-Pedret, Christian, additional, Palacios, Natalia Julia, additional, Lazaro, Ana, additional, Diez Tejedor, Exuperio, additional, Fernandez-Fournier, Mireya, additional, Lopez Ruiz, Pedro, additional, Rodriguez de Rivera, Francisco Javier, additional, Salvado Figueras, Maria, additional, Gamez, Josep, additional, Salvado, Maria, additional, Cortes Vicente, Elena, additional, Diaz-Manera, Jordi, additional, Querol Gutierrez, Luis, additional, Rojas Garcia, Ricardo, additional, Vidal, Nuria, additional, Arribas-Ibar, Elisabet, additional, Piehl, Fredrik, additional, Hietala, Albert, additional, Bjarbo, Lena, additional, Lindberg, Christopher, additional, Jons, Daniel, additional, Andersson, Blanka, additional, Sengun, Ihsan, additional, Ozcelik, Pinar, additional, Tuga, Celal, additional, Ugur, Muzeyyen, additional, Boz, Cavit, additional, Altiparmak, Didem, additional, Gazioglu, Sibel, additional, Ozen Aydin, Cigdem, additional, Erdem-Ozdamar, Sevim, additional, Bekircan-Kurt, Can Ebru, additional, Yilmaz, Ezgi, additional, Acar, Nazire Pinar, additional, Caliskan, Yagmur, additional, Efendi, Husnu, additional, Aydinlik, Seda, additional, Cavus, Hakan, additional, Semiz, Cansu, additional, Tun, Ozlem, additional, Terzi, Murat, additional, Dogan, Baki, additional, Onar, Musa Kazim, additional, Sen, Sedat, additional, Cavdar, Tugce Kirbas, additional, Norwood, Fiona, additional, Dimitriou, Aikaterini, additional, Gollogly, Jakit, additional, Mahdi-Rogers, Mohamed, additional, Seddigh, Arshira, additional, Maier, Gal, additional, Sohail, Faisal, additional, Sathasivam, Sivakumar, additional, Arndt, Heike, additional, Davies, Debbie, additional, Watling, Dave, additional, Rivner, Michael, additional, Hartmann, J. Edward, additional, Quarles, Brandy, additional, Smalley, Nicole, additional, Amato, Anthony, additional, Cochrane, Thomas, additional, Salajegheh, Mohammed, additional, Roe, Kristen, additional, Amato, Katherine, additional, Toska, Shirli, additional, Wolfe, Gil, additional, Silvestri, Nicholas, additional, Patrick, Kara, additional, Zakalik, Karen, additional, Katz, Jonathan, additional, Miller, Robert, additional, Engel, Marguerite, additional, Bravver, Elena, additional, Brooks, Benjamin, additional, Plevka, Sarah, additional, Burdette, Maryanne, additional, Sanjak, Mohammad, additional, Kramer, Megan, additional, Nemeth, Joanne, additional, Schommer, Clara, additional, Juel, Vern, additional, Guptill, Jeffrey, additional, Hobson-Webb, Lisa, additional, Beck, Kate, additional, Carnes, Donna, additional, Loor, John, additional, Anderson, Amanda, additional, Lange, Dale, additional, Agopian, Eliz, additional, Goldstein, Jonathan, additional, Manning, Erin, additional, Kaplan, Lindsay, additional, Holzberg, Shara, additional, Kassebaum, Nicole, additional, Pascuzzi, Robert, additional, Bodkin, Cynthia, additional, Kincaid, John, additional, Snook, Riley, additional, Guinrich, Sandra, additional, Micheels, Angela, additional, Chaudhry, Vinay, additional, Corse, Andrea, additional, Mosmiller, Betsy, additional, Ho, Doreen, additional, Srinivasan, Jayashri, additional, Vytopil, Michael, additional, Ventura, Nicholas, additional, Scala, Stephanie, additional, Carter, Cynthia, additional, Donahue, Craig, additional, Herbert, Carol, additional, Weiner, Elaine, additional, McKinnon, Jonathan, additional, Haar, Laura, additional, McKinnon, Naya, additional, Alcon, Karan, additional, Daniels, Kevin, additional, Sattar, Nadia, additional, Jeffery, Dennis, additional, McKenna, Kaitlyn, additional, Guidon, Amanda, additional, David, William, additional, Dheel, Christina, additional, Levine-Weinberg, Mark, additional, Nigro, Catherine, additional, Simpson, Ericka, additional, Appel, Stanley H, additional, Lai, Eugene, additional, Lay, Jr, Luis, additional, Pleitez, Milvia, additional, Halton, Sharon, additional, Faigle, Casey, additional, Thompson, Lisa, additional, Sivak, Mark, additional, Shin, Susan, additional, Bratton, Joan, additional, Jacobs, Daniel, additional, Brown, Gavin, additional, Bandukwala, Ibrez, additional, Brown, Morris, additional, Kane, Jennifer, additional, Blount, Ira, additional, Freimer, Miriam, additional, Hoyle, J. Chad, additional, Agriesti, Julie, additional, Khoury, Julie, additional, Marburger, Tessa, additional, Kaur, Harpreet, additional, Dimitrova, Diana, additional, Mellion, Michelle, additional, Sachs, George, additional, Crabtree, Brigid, additional, Keo, Roseann, additional, Perez, Ele Kim, additional, Taber, Sandra, additional, Gilchrist, James, additional, Andoin, Angela, additional, Darnell, Taylor, additional, Goyal, Neelam, additional, Sakamuri, Sarada, additional, So, Yuen T, additional, Welsh, Lesly Welsh, additional, Bhavaraju-Sanka, Ratna, additional, Tobon Gonzalez, Alejandro, additional, Jones, Floyd, additional, Saklad, Amy, additional, Nations, Sharon, additional, Trivedi, Jaya, additional, Hopkins, Steve, additional, Kazamel, Mohamed, additional, Alsharabati, Mohammad, additional, Lu, Liang, additional, Mumfrey-Thomas, Sandi, additional, Woodall, Amy, additional, Richman, David, additional, Butters, Janelle, additional, Lindsay, Molly, additional, Mozaffar, Tahseen, additional, Cash, Tiyonnoh, additional, Goyal, Namita, additional, Roy, Gulmohor, additional, Mathew, Veena, additional, Maqsood, Fatima, additional, Minton, Brian, additional, Jones, H. James, additional, Rosenfeld, Jeffrey, additional, Garcia, Rebekah, additional, Garcia, Sonia, additional, Echevarria, Laura, additional, Pulley, Michael, additional, Aranke, Shachie, additional, Berger, Alan Ross, additional, Shah, Jaimin, additional, Shabbir, Yasmeen, additional, Smith, Lisa, additional, Varghese, Mary, additional, Gutmann, Laurie, additional, Gutmann, Ludwig, additional, Swenson, Andrea, additional, Olalde, Heena, additional, Hafer-Macko, Charlene, additional, Kwan, Justin, additional, Zilliox, Lindsay, additional, Callison, Karen, additional, DiSanzo, Beth, additional, Naunton, Kerry, additional, Bilsker, Martin, additional, Sharma, Khema, additional, Reyes, Eliana, additional, Cooley, Anne, additional, Michon, Sara-Claude, additional, Steele, Julie, additional, Karam, Chafic Karam, additional, Chopra, Manisha, additional, Bird, Shawn, additional, Kaufman, Jacob, additional, Gallatti, Nichole, additional, Vu, Tuan, additional, Katzin, Lara, additional, McClain, Terry, additional, Harvey, Brittany, additional, Hart, Adam, additional, Huynh, Kristin, additional, Beydoun, Said, additional, Chilingaryan, Amaiak, additional, Droker, Brian, additional, Lin, Frank, additional, Shah, Akshay, additional, Tran, Anh, additional, Akhter, Salma, additional, Malekniazi, Ali, additional, Tandan, Rup, additional, Hehir, Michael, additional, Waheed, Waqar, additional, Lucy, Shannon, additional, Weiss, Michael, additional, Distad, Jane, additional, Downing, Sharon, additional, Strom, Susan, additional, Lisak, Robert, additional, Bernitsas, Evanthia, additional, Khan, Omar, additional, Kumar Sriwastava, Shitiz, additional, Tselis, Alexandros, additional, Jia, Kelly, additional, Bertorini, Tulio, additional, Arnold, Thomas, additional, Henderson, Kendrick, additional, Pillai, Rekha, additional, Liu, Ye, additional, Wheeler, Lauren, additional, Hewlett, Jasmine, additional, Vanderhook, Mollie, additional, Dicapua, Daniel, additional, Keung, Benison, additional, Kumar, Aditya, additional, Patwa, Huned, additional, Robeson, Kimberly, additional, Nye, Joan, additional, and Vu, Hong, additional
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- 2017
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25. Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
- Author
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McDonald, Craig M, primary, Campbell, Craig, additional, Torricelli, Ricardo Erazo, additional, Finkel, Richard S, additional, Flanigan, Kevin M, additional, Goemans, Nathalie, additional, Heydemann, Peter, additional, Kaminska, Anna, additional, Kirschner, Janbernd, additional, Muntoni, Francesco, additional, Osorio, Andrés Nascimento, additional, Schara, Ulrike, additional, Sejersen, Thomas, additional, Shieh, Perry B, additional, Sweeney, H Lee, additional, Topaloglu, Haluk, additional, Tulinius, Már, additional, Vilchez, Juan J, additional, Voit, Thomas, additional, Wong, Brenda, additional, Elfring, Gary, additional, Kroger, Hans, additional, Luo, Xiaohui, additional, McIntosh, Joseph, additional, Ong, Tuyen, additional, Riebling, Peter, additional, Souza, Marcio, additional, Spiegel, Robert J, additional, Peltz, Stuart W, additional, Mercuri, Eugenio, additional, Alfano, Lindsay N, additional, Eagle, Michelle, additional, James, Meredith K, additional, Lowes, Linda, additional, Mayhew, Anna, additional, Mazzone, Elena S, additional, Nelson, Leslie, additional, Rose, Kristy J, additional, Abdel-Hamid, Hoda Z, additional, Apkon, Susan D, additional, Barohn, Richard J, additional, Bertini, Enrico, additional, Bloetzer, Clemens, additional, de Vaud, Lausanne Canton, additional, Butterfield, Russell J, additional, Chabrol, Brigitte, additional, Chae, Jong-Hee, additional, Jongno-gu, Daehak-ro, additional, Comi, Giacomi Pietro, additional, Darras, Basil T, additional, Dastgir, Jahannaz, additional, Desguerre, Isabelle, additional, Escobar, Raul G, additional, Finanger, Erika, additional, Guglieri, Michela, additional, Hughes, Imelda, additional, Iannaccone, Susan T, additional, Jones, Kristi J, additional, Karachunski, Peter, additional, Kudr, Martin, additional, Lotze, Timothy, additional, Mah, Jean K, additional, Mathews, Katherine, additional, Nevo, Yoram, additional, Parsons, Julie, additional, Péréon, Yann, additional, de Queiroz Campos Araujo, Alexandra Prufer, additional, Renfroe, J Ben, additional, de Resende, Maria Bernadete Dutra, additional, Ryan, Monique, additional, Selby, Kathryn, additional, Tennekoon, Gihan, additional, and Vita, Giuseppe, additional
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- 2017
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26. Developing standardized corticosteroid treatment for Duchenne muscular dystrophy
- Author
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Guglieri, Michela, primary, Bushby, Kate, additional, McDermott, Michael P., additional, Hart, Kimberly A., additional, Tawil, Rabi, additional, Martens, William B., additional, Herr, Barbara E., additional, McColl, Elaine, additional, Wilkinson, Jennifer, additional, Kirschner, Janbernd, additional, King, Wendy M., additional, Eagle, Michele, additional, Brown, Mary W., additional, Willis, Tracey, additional, Hirtz, Deborah, additional, Shieh, Perry B., additional, Straub, Volker, additional, Childs, Anne-Marie, additional, Ciafaloni, Emma, additional, Butterfield, Russell J., additional, Horrocks, Iain, additional, Spinty, Stefan, additional, Flanigan, Kevin M., additional, Kuntz, Nancy L., additional, Baranello, Giovanni, additional, Roper, Helen, additional, Morrison, Leslie, additional, Mah, Jean K., additional, Manzur, Adnan Y., additional, McDonald, Craig M., additional, Schara, Ulrike, additional, von der Hagen, Maja, additional, Barohn, Richard J., additional, Campbell, Craig, additional, Darras, Basil T., additional, Finkel, Richard S., additional, Vita, Giuseppe, additional, Hughes, Imelda, additional, Mongini, Tiziana, additional, Pegoraro, Elena, additional, Wicklund, Matthew, additional, Wilichowski, Ekkehard, additional, Bryan Burnette, W., additional, Howard, James F., additional, McMillan, Hugh J., additional, Thangarajh, Mathula, additional, and Griggs, Robert C., additional
- Published
- 2017
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27. Rare variants in SQSTM1 and VCP genes and risk of sporadic inclusion body myositis
- Author
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Gang, Qiang, primary, Bettencourt, Conceição, additional, Machado, Pedro M., additional, Brady, Stefen, additional, Holton, Janice L., additional, Pittman, Alan M., additional, Hughes, Deborah, additional, Healy, Estelle, additional, Parton, Matthew, additional, Hilton-Jones, David, additional, Shieh, Perry B., additional, Needham, Merrilee, additional, Liang, Christina, additional, Zanoteli, Edmar, additional, de Camargo, Leonardo Valente, additional, De Paepe, Boel, additional, De Bleecker, Jan, additional, Shaibani, Aziz, additional, Ripolone, Michela, additional, Violano, Raffaella, additional, Moggio, Maurizio, additional, Barohn, Richard J., additional, Dimachkie, Mazen M., additional, Mora, Marina, additional, Mantegazza, Renato, additional, Zanotti, Simona, additional, Singleton, Andrew B., additional, Hanna, Michael G., additional, Houlden, Henry, additional, Gang, Qiang, additional, Bettencourt, Conceicao, additional, McVey, April L., additional, Pasnoor, Mamatha, additional, Glenn, Melanie, additional, Jawdat, Omar, additional, Statland, Jeffrey, additional, Rico, Gabrielle, additional, Mastaglia, Frank, additional, Dalakas, Marinos C., additional, Biba, Angie, additional, Chinoy, Hector, additional, Lilleker, James B., additional, Lamb, Janine, additional, Platt, Hazel, additional, Cooper, Robert G., additional, Miller, James A.L., additional, Roberts, Mark, additional, Househam, Elizabeth, additional, Hilton, David, additional, Shivane, Aditya, additional, Bartlett, Amy, additional, Kissel, John T., additional, Runk, Heidi, additional, Wicklund, Matthew, additional, Saperstein, David S., additional, and McKinney, Lynette R., additional
- Published
- 2016
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28. Prospective exploratory muscle biopsy, imaging, and functional assessment in patients with late-onset Pompe disease treated with alglucosidase alfa: The EMBASSY Study
- Author
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van der Ploeg, Ans, primary, Carlier, Pierre G., additional, Carlier, Robert-Yves, additional, Kissel, John T., additional, Schoser, Benedikt, additional, Wenninger, Stephan, additional, Pestronk, Alan, additional, Barohn, Richard J., additional, Dimachkie, Mazen M., additional, Goker-Alpan, Ozlem, additional, Mozaffar, Tahseen, additional, Pena, Loren D.M., additional, Simmons, Zachary, additional, Straub, Volker, additional, Guglieri, Michela, additional, Young, Peter, additional, Boentert, Matthias, additional, Baudin, Pierre-Yves, additional, Wens, Stephan, additional, Shafi, Raheel, additional, Bjartmar, Carl, additional, and Thurberg, Beth L., additional
- Published
- 2016
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29. Motor Neuron Disease
- Author
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Dimachkie, Mazen M., primary and Barohn, Richard J., additional
- Published
- 2015
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30. Patterns of Weakness, Classification of Motor Neuron Disease, and Clinical Diagnosis of Sporadic Amyotrophic Lateral Sclerosis
- Author
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Statland, Jeffrey M., primary, Barohn, Richard J., additional, McVey, April L., additional, Katz, Jonathan S., additional, and Dimachkie, Mazen M., additional
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- 2015
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31. The Dilemma of the Clinical Trialist in Amyotrophic Lateral Sclerosis
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Katz, Jonathan S., primary, Barohn, Richard J., additional, Dimachkie, Mazen M., additional, and Mitsumoto, Hiroshi, additional
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- 2015
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32. Amyotrophic Lateral Sclerosis Regional Variants (Brachial Amyotrophic Diplegia, Leg Amyotrophic Diplegia, and Isolated Bulbar Amyotrophic Lateral Sclerosis)
- Author
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Jawdat, Omar, primary, Statland, Jeffrey M., additional, Barohn, Richard J., additional, Katz, Jonathan S., additional, and Dimachkie, Mazen M., additional
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- 2015
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33. Symptom Management and End-of-Life Care in Amyotrophic Lateral Sclerosis
- Author
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Jackson, Carlayne E., primary, McVey, April L., additional, Rudnicki, Stacy, additional, Dimachkie, Mazen M., additional, and Barohn, Richard J., additional
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- 2015
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34. Amyotrophic Lateral Sclerosis
- Author
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Katz, Jonathan S., primary, Dimachkie, Mazen M., additional, and Barohn, Richard J., additional
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- 2015
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35. Primary Lateral Sclerosis
- Author
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Statland, Jeffrey M., primary, Barohn, Richard J., additional, Dimachkie, Mazen M., additional, Floeter, Mary Kay, additional, and Mitsumoto, Hiroshi, additional
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- 2015
- Full Text
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36. Disease course and therapeutic approach in dermatomyositis: A four-center retrospective study of 100 patients
- Author
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Johnson, Nicholas E., primary, Arnold, W. David, additional, Hebert, Donald, additional, Gwathmey, Kelly, additional, Dimachkie, Mazen M., additional, Barohn, Richard J., additional, McVey, April L., additional, Pasnoor, Mamatha, additional, Amato, Anthony A., additional, McDermott, Michael P., additional, Kissel, John, additional, and Heatwole, Chad R., additional
- Published
- 2015
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37. The effects of an intronic polymorphism in TOMM40 and APOE genotypes in sporadic inclusion body myositis
- Author
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Gang, Qiang, primary, Bettencourt, Conceicao, additional, Machado, Pedro M., additional, Fox, Zoe, additional, Brady, Stefen, additional, Healy, Estelle, additional, Parton, Matt, additional, Holton, Janice L., additional, Hilton-Jones, David, additional, Shieh, Perry B., additional, Zanoteli, Edmar, additional, De Paepe, Boel, additional, De Bleecker, Jan, additional, Shaibani, Aziz, additional, Ripolone, Michela, additional, Violano, Raffaella, additional, Moggio, Maurizio, additional, Barohn, Richard J., additional, Dimachkie, Mazen M., additional, Mora, Marina, additional, Mantegazza, Renato, additional, Zanotti, Simona, additional, Hanna, Michael G., additional, and Houlden, Henry, additional
- Published
- 2015
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38. A phase 4 prospective study in patients with adult Pompe disease treated with alglucosidase alfa
- Author
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Thurberg, Beth L., primary, Carlier, Pierre, additional, Kissel, John T., additional, Schoser, Benedikt, additional, Pestronk, Alan, additional, Barohn, Richard, additional, Goker-Alpan, Ozlem, additional, Mozaffar, Tahseen, additional, Pena, Loren D.M., additional, Simmons, Zachary, additional, Straub, Volker, additional, Young, Peter, additional, Shafi, Raheel, additional, Bjartmar, Carl, additional, and van der Ploeg, Ans, additional
- Published
- 2015
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39. A Pattern Recognition Approach to Patients with a Suspected Myopathy
- Author
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Barohn, Richard J., primary, Dimachkie, Mazen M., additional, and Jackson, Carlayne E., additional
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- 2014
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40. Toxic Myopathies
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Pasnoor, Mamatha, primary, Barohn, Richard J., additional, and Dimachkie, Mazen M., additional
- Published
- 2014
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- View/download PDF
41. Inclusion Body Myositis
- Author
-
Dimachkie, Mazen M., primary and Barohn, Richard J., additional
- Published
- 2014
- Full Text
- View/download PDF
42. Idiopathic Inflammatory Myopathies
- Author
-
Dimachkie, Mazen M., primary, Barohn, Richard J., additional, and Amato, Anthony A., additional
- Published
- 2014
- Full Text
- View/download PDF
43. Myopathies
- Author
-
Dimachkie, Mazen M., primary and Barohn, Richard J., additional
- Published
- 2014
- Full Text
- View/download PDF
44. Pompe Disease
- Author
-
Dasouki, Majed, primary, Jawdat, Omar, additional, Almadhoun, Osama, additional, Pasnoor, Mamatha, additional, McVey, April L., additional, Abuzinadah, Ahmad, additional, Herbelin, Laura, additional, Barohn, Richard J., additional, and Dimachkie, Mazen M., additional
- Published
- 2014
- Full Text
- View/download PDF
45. Distal Myopathies
- Author
-
Dimachkie, Mazen M., primary and Barohn, Richard J., additional
- Published
- 2014
- Full Text
- View/download PDF
46. Preliminary clinical efficacy and safety of BMN 701, GILT-tagged recombinant human acid alpha glucosidase (rhGAA), in late-onset Pompe disease: results of an extension study
- Author
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Byrne, Barry, primary, Barohn, Richard, additional, Barshop, Bruce, additional, Bratkovic, Drago, additional, Desnuelle, Claude, additional, Henderson, Robert, additional, Hiwot, Tarekegn, additional, Hughes, Derralynn, additional, Laforet, Pascal, additional, Mengel, Eugen, additional, Roberts, Mark, additional, Lang, William, additional, and LeBowitz, Jonathon, additional
- Published
- 2014
- Full Text
- View/download PDF
47. Pattern-Recognition Approach to Neuropathy and Neuronopathy
- Author
-
Barohn, Richard J., primary and Amato, Anthony A., additional
- Published
- 2013
- Full Text
- View/download PDF
48. Multifocal Motor Neuropathy, Multifocal Acquired Demyelinating Sensory and Motor Neuropathy, and Other Chronic Acquired Demyelinating Polyneuropathy Variants
- Author
-
Dimachkie, Mazen M., primary, Barohn, Richard J., additional, and Katz, Jonathan, additional
- Published
- 2013
- Full Text
- View/download PDF
49. Guillain-Barré Syndrome and Variants
- Author
-
Dimachkie, Mazen M., primary and Barohn, Richard J., additional
- Published
- 2013
- Full Text
- View/download PDF
50. Nutritional Neuropathies
- Author
-
Hammond, Nancy, primary, Wang, Yunxia, additional, Dimachkie, Mazen M., additional, and Barohn, Richard J., additional
- Published
- 2013
- Full Text
- View/download PDF
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