24 results on '"Onodera, Masafumi"'
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2. Melting temperature mapping method in children: Rapid identification of pathogenic microbes
3. A novel mucopolysaccharidosis type II mouse model with an iduronate-2-sulfatase-P88L mutation
4. Myelodysplasia after clonal hematopoiesis with APOBEC3-mediated CYBB inactivation in retroviral gene therapy for X-CGD
5. Enhanced osteoblastic differentiation of parietal bone in a novel murine model of mucopolysaccharidosis type II
6. Corrigendum to “Enhanced osteoblastic differentiation of parietal bone in a novel murine model of mucopolysaccharidosis type II” [Molecular Genetics and Metabolism Reports Vol. 37, December 2023, 101021]
7. Melting temperature mapping method in children: Rapid identification of pathogenic microbes
8. Chromosomal translocation t(11;14) and p53 deletion induced by the CRISPR/Cas9 system in normal B cell-derived iPS cells
9. Peripheral immune system modulates Purkinje cell degeneration in Niemann–Pick disease type C1
10. Ferroptosis model system by the re-expression of BACH1
11. National Survey on Clinical Practice of Gene Therapy using Adeno-associated Virus Vector ―The Actual Status and Hurdle on Clinical Practice in Gene Therapy for Spinal Muscular Atrophy―
12. Attempts to Induce t(11;14) during Redifferentiation of Normal B Cell-Derived Ips Cells to Study Myeloma-Initiating Cells
13. LBODP008 Gene Therapy For Congenital Adrenal Hyperplasia With AAV Vectors Into Fibroblasts, IPS Cells And Model Mice
14. Adeno-Associated Virus-Mediated Gene Therapy for Patients' Fibroblasts, Induced Pluripotent Stem Cells, and a Mouse Model of Congenital Adrenal Hyperplasia
15. Safety and efficacy of elapegademase in patients with adenosine deaminase deficiency: A multicenter, open‐label, single‐arm, phase 3, and postmarketing clinical study.
16. Nonconditioned ADA-SCID gene therapy reveals ADA requirement in the hematopoietic system and clonal dominance of vector-marked clones
17. Normal B Cell-Derived iPSCs Capable of Inducing RAS Mutants and Aid to Explore Myeloma-Initiating Cells
18. Evaluation methods for biodistribution, safety and efficacy of gene therapy products
19. Production of therapeutic iduronate‐2‐sulfatase enzyme with a novel single‐stranded RNA virus vector.
20. Bacillus Calmette-Guérin (BCG) Infections at High Frequency in Both AR-CGD and X-CGD Patients Following BCG Vaccination.
21. A Non-targeted Proteomics Newborn Screening Platform for Inborn Errors of Immunity.
22. Improving the Assessment of Risk Factors Relevant to Potential Carcinogenicity of Gene Therapies: A Consensus Article.
23. Successful hematopoietic stem cell transplantation with reduced dose of busulfan for Omenn syndrome.
24. Nonconditioned ADA-SCID gene therapy reveals ADA requirement in the hematopoietic system and clonal dominance of vector-marked clones.
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