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Your search keyword '"Muscular Atrophy, Spinal drug therapy"' showing total 10 results
Start Over Descriptor "Muscular Atrophy, Spinal drug therapy" Publication Type Magazines
10 results on '"Muscular Atrophy, Spinal drug therapy"'

1. First small-molecule drug targeting RNA gains momentum.

Author

Sheridan C

Subjects
Azo Compounds pharmacology, Azo Compounds therapeutic use, Gene Expression drug effects, Humans, Muscular Atrophy, Spinal drug therapy, Neuromuscular Agents pharmacology, Neuromuscular Agents therapeutic use, Pyrimidines pharmacology, Pyrimidines therapeutic use, Drug Delivery Systems, RNA drug effects, RNA metabolism
Published
2021
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2. Upcoming market catalysts in Q3 2020.

Author

Eisold A

Subjects
Angelman Syndrome drug therapy, Fatty Acids metabolism, Humans, Muscular Atrophy, Spinal drug therapy, United States, Azo Compounds administration & dosage, Drug Approval economics, Isoxazoles administration & dosage, Pyrimidines administration & dosage, Triglycerides administration & dosage
Published
2020
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3. ASO Therapy: Hope for Genetic Neurological Diseases.

Author

Muth CC

Subjects
Animals, Disease Models, Animal, Humans, Mice, Muscular Atrophy, Spinal genetics, Muscular Dystrophy, Duchenne drug therapy, Muscular Dystrophy, Duchenne genetics, Mutation, Neurodegenerative Diseases genetics, Spinocerebellar Ataxias drug therapy, Muscular Atrophy, Spinal drug therapy, Neurodegenerative Diseases drug therapy, Oligonucleotides, Antisense therapeutic use
Published
2018
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4. Bringing RNA into the fold: Small molecules find new targets in RNA to combat disease.

Author

Chakradhar S

Subjects
Catalysis, Drug Discovery, Humans, Infections drug therapy, Inflammation drug therapy, Muscular Atrophy, Spinal drug therapy, Neurodegenerative Diseases drug therapy, Nucleic Acid Conformation, RNA metabolism, RNA, Catalytic metabolism, Rare Diseases drug therapy, Small Molecule Libraries chemistry, Structure-Activity Relationship, Drug Delivery Systems, RNA chemistry, Small Molecule Libraries pharmacology
Published
2017
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5. Spinal muscular atrophy approval boosts antisense drugs.

Author

Dolgin E

Subjects
Drug Approval, Drug Industry economics, Drug Industry legislation & jurisprudence, Humans, United States, United States Food and Drug Administration, Muscular Atrophy, Spinal drug therapy, Oligonucleotides, Antisense economics, Oligonucleotides, Antisense therapeutic use
Published
2017
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6. Drugs that made headlines in 2016.

Author

Keener AB

Subjects
Clinical Trials as Topic, Drug Discovery, Drug Therapy, Europe, Genetic Therapy, Health Policy, Humans, Muscular Atrophy, Spinal drug therapy, Nucleotides chemistry, United States, United States Food and Drug Administration, Drug Approval, Drug Industry trends, Pharmaceutical Preparations
Published
2016
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8. Call in the backup.

Author

Dolgin E

Subjects
Drug Industry, Gene Dosage, Genome, Human, Heterozygote, Histone Deacetylase Inhibitors therapeutic use, Histone Deacetylases administration & dosage, Humans, Infant, Newborn, Molecular Targeted Therapy, Motor Neurons drug effects, Mutation, Survival of Motor Neuron 1 Protein therapeutic use, Survival of Motor Neuron 2 Protein genetics, Survival of Motor Neuron 2 Protein therapeutic use, Clinical Trials as Topic, Motor Neurons metabolism, Muscular Atrophy, Spinal drug therapy, Survival of Motor Neuron 1 Protein genetics
Published
2012
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9. Stem cells: Tailor-made diseased neurons.

Author

Sendtner M

Subjects
Animals, Cell Separation, Child, Female, Fibroblasts cytology, Humans, Mice, Models, Biological, Motor Neurons drug effects, Motor Neurons metabolism, Muscular Atrophy, Spinal drug therapy, Muscular Atrophy, Spinal metabolism, Pluripotent Stem Cells cytology, Pluripotent Stem Cells drug effects, Pluripotent Stem Cells metabolism, Survival of Motor Neuron 1 Protein genetics, Survival of Motor Neuron 1 Protein metabolism, Cell Differentiation drug effects, Cellular Reprogramming drug effects, Motor Neurons pathology, Muscular Atrophy, Spinal pathology, Pluripotent Stem Cells pathology, Skin cytology
Published
2009
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10. Targeting toxic proteins for turnover.

Author

La Spada AR and Weydt P

Subjects
Animals, Benzoquinones, Disease Models, Animal, HSP90 Heat-Shock Proteins metabolism, Lactams, Macrocyclic, Mice, Muscular Atrophy, Spinal genetics, Peptides genetics, Rifabutin pharmacology, Rifabutin therapeutic use, Trinucleotide Repeat Expansion genetics, HSP90 Heat-Shock Proteins antagonists & inhibitors, Muscular Atrophy, Spinal drug therapy, Muscular Atrophy, Spinal pathology, Receptors, Androgen genetics, Receptors, Androgen metabolism, Rifabutin analogs & derivatives
Published
2005
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