1. [SFGM-TC recommendation on indications for allogeneic stem cell transplantation in children with congenital neutropenia].
- Author
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Dalle JH, Donadieu J, Paillard C, Rialland F, Schneider P, Sicre De Fontbrune F, Hichri Y, Neven B, and Yakoub-Agha I
- Subjects
- Adolescent, Bone Marrow Diseases complications, Bone Marrow Diseases surgery, Child, Child, Preschool, Congenital Bone Marrow Failure Syndromes, Exocrine Pancreatic Insufficiency complications, Exocrine Pancreatic Insufficiency surgery, France, Humans, Infant, Infections, Leukemia, Lipomatosis complications, Lipomatosis surgery, Neutropenia complications, Risk Factors, Shwachman-Diamond Syndrome, Stem Cell Transplantation standards, Transplantation, Homologous standards, Neutropenia congenital, Neutropenia surgery, Stem Cell Transplantation methods, Transplantation, Homologous methods
- Abstract
In this report, we address the issue of allogeneic stem cell transplantation in children with congenital neutropenia. Constitutional disorders with neutropenia are exceptional. Treatment and prevention of severe infections are a major concern in the management of chronic neutropenia. These disorders, especially Kostmann's disease and Shwachman-Bodian-Diamond syndrome, are associated with an increased risk of leukemia. The role of allogeneic stem cell transplantation in these patients is still unclear. In an effort to harmonize clinical practices between different French transplantation centers, the French Society of Bone Marrow Transplantation and Cell Therapy (SFGM-TC) set up the fourth annual series of workshops which brought together practitioners from all member centers and took place in September 2013 in Lille., (Copyright © 2014 Elsevier Masson SAS. All rights reserved.)
- Published
- 2014
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