8 results on '"Pierson, Tyler Mark"'
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2. Human induced pluripotent stem cell models for CLN6
3. Modeling CLN6 with IPSC-derived neural cells
4. Modeling CLN6 with patient-derived IPS cells
5. Hereditary spastic paraplegias types 15 and 11 are associated with lysosomal abnormalities
6. Juvenile-onset motor neuron disease caused by novel mutations in β-hexosaminidase
7. Unrelated umbilical cord blood transplant for juvenile metachromatic leukodystrophy: A 5-year follow-up in three affected siblings
8. 74. Novel mutations in juvenile Sandhoff disease presenting as motor neuron disease
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