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3. Increased prevalence of Parkinson's disease in alkaptonuria

4. Outcome of infantile nephropathic cystinosis depends on early intervention, not genotype: A multicenter sibling cohort study

6. Multi‐omics in classical galactosemia: Evidence for the involvement of multiple metabolic pathways

9. Neurocognitive outcome and mental health in children with tyrosinemia type 1 and phenylketonuria: A comparison between two genetic disorders affecting the same metabolic pathway

15. Targeting the Diagnosis in an Adolescent with Epilepsy and Intellectual Disability through Next-Generation Metabolic Screening

17. Serum GDF15 Levels Correlate to Mitochondrial Disease Severity and Myocardial Strain, but Not to Disease Progression in Adult m.3243A>G Carriers

19. Natural history, outcome measures and trial readiness in LAMA2-related muscular dystrophy and SELENON-related myopathy in children and adults: protocol of the LAST STRONG study

21. Inheritance of the m.3243A>G mutation

23. A predictive model for estimating the number of erythrocytapheresis or phlebotomy treatments for patients with naïve hereditary hemochromatosis

24. Monitoring phenylalanine concentrations in the follow‐up of phenylketonuria patients: An inventory of pre‐analytical and analytical variation

26. Correction to: Classical galactosemia: neuropsychological and psychosocial functioning beyond intellectual abilities

30. Classical galactosemia: neuropsychological and psychosocial functioning beyond intellectual abilities

31. The 1‐ 13 C galactose breath test in GALT deficient patients distinguishes NBS detected variant patients but does not predict outcome in classical phenotypes

32. Deep phenotyping classical galactosemia: clinical outcomes and biochemical markers

34. Movement disorders and nonmotor neuropsychological symptoms in children and adults with classical galactosemia

39. Next-generation metabolic screening: targeted and untargeted metabolomics for the diagnosis of inborn errors of metabolism in individual patients

42. Long-Term Follow-Up of Cognition and Mental Health in Adult Phenylketonuria: A PKU-COBESO Study

43. Cognitive profile and mental health in adult phenylketonuria: A PKU-COBESO study.

44. International Paediatric Mitochondrial Disease Scale

45. Social-cognitive functioning and social skills in patients with early treated phenylketonuria: a PKU-COBESO study

46. High prevalence of complementary and alternative medicine use in patients with genetically proven mitochondrial disorders

48. Reduced response of Cystathionine Beta-Synthase (CBS) to S-Adenosylmethionine (SAM): Identification and functional analysis of CBS gene mutations in Homocystinuria patients

49. Erratum: Symptomatic lipid storage in carriers for the PNPLA2 gene

50. Symptomatic lipid storage in carriers for the PNPLA2 gene

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