68 results on '"Boye, Shannon E."'
Search Results
2. Development of an AAV-CRISPR-Cas9-based treatment for dominant cone-rod dystrophy 6
3. Dual-AAV vector mediated expression of MYO7A improves vestibular function in a mouse model of Usher Syndrome 1B
4. Correction: Site-specific modifications to AAV8 capsid yields enhanced brain transduction in the neonatal MPS IIIB mouse
5. SubILM Injection of AAV for Gene Delivery to the Retina
6. Improving retinal vascular endothelial cell tropism through rational rAAV capsid design
7. Preclinical studies in support of phase I/II clinical trials to treat GUCY2D-associated Leber congenital amaurosis
8. Improving retinal vascular endothelial cell tropism through rational rAAV capsid design
9. Identifying and Overcoming Challenges in Developing Effective Treatments for Usher 1B: A Workshop Report
10. Post-developmental plasticity of the primary rod pathway allows restoration of visually guided behaviors
11. Night vision restored in days after decades of congenital blindness
12. Gene Therapy in Opn1mw−/−/Opn1sw−/− Mice and Implications for Blue Cone Monochromacy Patients with Deletion Mutations
13. A Mini-review: Animal Models of GUCY2D Leber Congenital Amaurosis (LCA1)
14. Cone Specific Promoter for Use in Gene Therapy of Retinal Degenerative Diseases
15. Safety and improved efficacy signals following gene therapy in childhood blindness caused by GUCY2D mutations
16. Effects of Altering Heparan Sulfate Proteoglycan Binding and Capsid Hydrophilicity on Retinal Transduction by Adeno-associated Virus
17. Retinal Diseases
18. Current Clinical Applications of In Vivo Gene Therapy with AAVs
19. Site-specific modifications to AAV8 capsid yields enhanced brain transduction in the neonatal MPS IIIB mouse
20. SARM1 depletion rescues NMNAT1-dependent photoreceptor cell death and retinal degeneration
21. Author response: SARM1 depletion rescues NMNAT1-dependent photoreceptor cell death and retinal degeneration
22. Identifying Treatments for Taste and Smell Disorders: Gaps and Opportunities
23. Novel AAV44.9-Based Vectors Display Exceptional Characteristics for Retinal Gene Therapy
24. SARM1 depletion rescues NMNAT1 dependent photoreceptor cell death and retinal degeneration
25. Adeno-Associated Virus D-Sequence-Mediated Suppression of Expression of a Human Major Histocompatibility Class II Gene: Implications in the Development of Adeno-Associated Virus Vectors for Modulating Humoral Immune Response
26. Utilizing minimally purified secreted rAAV for rapid and cost-effective manipulation of gene expression in the CNS
27. A Novel Mouse Model of MYO7A USH1B Reveals Auditory and Visual System Haploinsufficiencies
28. Somatic Gene Editing of GUCY2D by AAV-CRISPR/Cas9 Alters Retinal Structure and Function in Mouse and Macaque
29. A Drug-Tunable Gene Therapy for Broad-Spectrum Protection against Retinal Degeneration
30. A drug-tunable gene therapy for broad-spectrum protection against retinal degeneration
31. Rationally Engineered AAV Capsids Improve Transduction and Volumetric Spread in the CNS
32. Optimization of Retinal Gene Therapy for X-Linked Retinitis Pigmentosa Due to RPGR Mutations
33. Defining Outcomes for Clinical Trials of Leber Congenital Amaurosis Caused by GUCY2D Mutations
34. The GCaMP-R Family of Genetically Encoded Ratiometric Calcium Indicators
35. Increased vulnerability of photoreceptors to aberrant splicing highlight the utility of AON-based therapy for CEP290-LCA
36. Novel Methodology for Creating Macaque Retinas with Sortable Photoreceptors and Ganglion Cells
37. NF1 Is a Direct G Protein Effector Essential for Opioid Signaling to Ras in the Striatum
38. Highly Efficient Delivery of Adeno-Associated Viral Vectors to the Primate Retina
39. 620. Use of Transgenic Mice to Quantify Transduction Efficiency and Specificity of Novel AAV Vectors in Retina
40. Impact of Heparan Sulfate Binding on Transduction of Retina by Recombinant Adeno-Associated Virus Vectors
41. Targeting the Nrf2 Signaling Pathway in the Retina With a Gene-Delivered Secretable and Cell-Penetrating Peptide
42. Cone-Specific Promoters for Gene Therapy of Achromatopsia and Other Retinal Diseases
43. Systemic Vascular Transduction by Capsid Mutant Adeno-Associated Virus After Intravenous Injection
44. Gene Therapy Fully Restores Vision to the All-Cone Nrl−/−Gucy2e−/− Mouse Model of Leber Congenital Amaurosis-1
45. Intravitreal delivery of a novel AAV vector targets ON bipolar cells and restores visual function in a mouse model of complete congenital stationary night blindness
46. Capsid Mutated Adeno-Associated Virus Delivered to the Anterior Chamber Results in Efficient Transduction of Trabecular Meshwork in Mouse and Rat
47. Gene Therapy With the Caspase Activation and Recruitment Domain Reduces the Ocular Inflammatory Response
48. 498. Optimization of rAAV Targets ON Bipolar Cells and Rescues the nobnyx Mouse Model of X-Linked Congenital Stationary Night Blindness
49. Targeted Gene Delivery to the Enteric Nervous System Using AAV: A Comparison Across Serotypes and Capsid Mutants
50. Gene Delivery of a Viral Anti-Inflammatory Protein to Combat Ocular Inflammation
Catalog
Books, media, physical & digital resources
Discovery Service for Jio Institute Digital Library
For full access to our library's resources, please sign in.