587 results on '"Muscular dystrophies"'
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2. Assessments in Patients With Muscular Pathology and in Control Subjects : The ActiLiège Next Study
3. A Study of ATL1102 or Placebo in Participants With Non-ambulatory Duchenne Muscular Dystrophy
4. An Observational Study Comparing Delandistrogene Moxeparvovec With Standard of Care in Participants With Duchenne Muscular Dystrophy (ENDURE)
5. A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene Xeboparvovec (SRP-9003) as a Possible Treatment for Limb Girdle Muscular Dystrophy 2E/R4 (EMERGENE)
6. A Gene Delivery Study to Evaluate the Safety and Expression of Delandistrogene Moxeparvovec in Participants Under the Age of Four With Duchenne Muscular Dystrophy (DMD) (ENVOL)
7. Comparative Effects of Clamshell Technique With EMS vs CTin Iliotibial Band Tightness for Pain and Function
8. A Gene Transfer Therapy Study to Evaluate the Safety of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)
9. Quantitative Assessment of Orofacial Muscle Function in FSHD
10. AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD)
11. Global Study of Del-desiran for the Treatment of DM1 (HARBOR)
12. Long-Term Development of Muscular Dystrophy Outcome Assessments (GRASP-01-005)
13. A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical Study (EXPEDITION)
14. Registry of Translarna (Ataluren) in Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)
15. Psychoeducation Program for Parents of Children With DMD
16. A Study Of PGN-EDO51 In Participants With Duchenne Muscular Dystrophy Amenable To Exon 51-Skipping Treatment (CONNECT1-EDO51)
17. Open-Label Extension of EDG-5506 in Participants With Becker Muscular Dystrophy (MESA)
18. Study to Evaluate the Efficacy and Safety of BBP-418 (Ribitol) in Patients With Limb Girdle Muscular Dystrophy 2I (LGMD2I) (Fortify)
19. Phase 2 Study of EDG-5506 in Becker Muscular Dystrophy (GRAND CANYON)
20. Effectiveness of a Multimodal Physiotherapy Program With Virtual Reality Glasses in Duchenne and Becker. (RVDuchenne)
21. A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Non-Ambulatory and Ambulatory Participants With Duchenne Muscular Dystrophy (DMD) (ENVISION)
22. Gamified Occupational Therapy for Adolescents With Duchenne Muscular Dystrophy (DMD)
23. The United Kingdom Facioscapulohumeral Muscular Dystrophy Patient Registry
24. A Study to Evaluate the Safety and Tolerability of GEN6050X in Duchenne Muscular Dystrophy. (GEN6050XIIT)
25. Trial Readiness and Endpoint Assessment in LGMD R1 (GRASP-01-003)
26. Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-251 in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51 Skipping (DELIVER)
27. The Role of Muscle Ultrasound in Assessment of Sample of Patients With Limb-girdle Muscular Dystrophy
28. Oral Ifetroban in Subjects With Duchenne Muscular Dystrophy (DMD)
29. Genetic and Physical Study of Childhood Nerve and Muscle Disorders
30. Defining Endpoints in Becker Muscular Dystrophy (GRASP-01-002)
31. A Study to Assess Vamorolone in Boys Ages 2 to <4 Years and 7 to <18 Years With Duchenne Muscular Dystrophy (DMD)
32. Defining Clinical Endpoints in Limb Girdle Muscular Dystrophy (LGMD) (GRASP-01-001)
33. Parent and Infant Inter(X)Action Intervention (PIXI)
34. Evolution of the Functional and Muscular State of Patients With Muscular Dystrophy 2A Belts (CALNATHIS)
35. Study of Inherited Neurological Disorders
36. Upper Extremity Muscle Strength, Balance and Functional Skills in DMD
37. Study of AOC 1044 in Healthy Adult Volunteers and Participants With Duchenne Muscular Dystrophy (DMD) Mutations Amenable to Exon 44 Skipping (EXPLORE44)
38. Halt cardiomyOPathy progrEssion in Duchenne (HOPE-OLE) (HOPE-OLE)
39. A Study to Evaluate RO7204239 in Participants With Facioscapulohumeral Muscular Dystrophy (MANOEUVRE)
40. Study of Ataluren in Previously Treated Participants With Nonsense Mutation Dystrophinopathy (nmDBMD)
41. COMMAND Early Feasibility Study: Implantable BCI to Control a Digital Device for People With Paralysis
42. Rehabilitation in Muscular Dystrophies From the Hospital Facility to the Home: Pilot Project [RIMUDI] (RIMUDI)
43. At-Home Research Study for Patients With Autoimmune, Inflammatory, Genetic, Hematological, Infectious, Neurological, CNS, Oncological, Respiratory, Metabolic Conditions
44. Wearable Technology to Evaluate Hyperglycemia and HRV in DMD - Longitudinal Aim
45. phenotypeS in Non Ambulant Duchenne Muscular Dystrophy (GUP21003)
46. A Phase 1/2 Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of BMN 351 in Participants With Duchenne Muscular Dystrophy
47. Assessment of Neurodevelopmental Needs in Duchenne Muscular Dystrophy
48. A Study to Compare Safety and Efficacy of a High Dose of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) (MIS51ON)
49. The Effect of a Muscle-mimicking, Fabric-type Shoulder Orthosis on Functional Movements of the Upper Limb in Patients With Duchenne Muscular Dystrophy
50. Effectiveness of 5-week Digital Respiratory Practice in a Group of Children With Duchenne Muscular Dystrophy and Becker Muscular Dystrophy. (DMDrespy2024)
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